Assessment of the reliability, responsiveness, and meaningfulness of the scale for the assessment and rating of ataxia (SARA) for lysosomal storage disorders
评估溶酶体贮积症共济失调评估和评级量表(SARA)的信度、反应性和意义
期刊:Journal of Neurology
影响因子:4.6
doi:10.1007/s00415-024-12664-y
Park, Julien; Bremova-Ertl, Tatiana; Brands, Marion; Foltan, Tomas; Gautschi, Matthias; Gissen, Paul; Hahn, Andreas; Jones, Simon; Arash-Kaps, Laila; Kolnikova, Miriam; Patterson, Marc; Perlman, Susan; Ramaswami, Uma; Reichmannová, Stella; Rohrbach, Marianne; Schneider, Susanne A; Shaikh, Aasef; Sivananthan, Siyamini; Synofzik, Matthis; Walterfarng, Mark; Wibawa, Pierre; Martakis, Kyriakos; Manto, Mario