日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Nonclinical evaluation of renizgamglogene autogedtemcel for SCD and TDT.

对 renizgamglogene autogedtemcel 治疗 SCD 和 TDT 的非临床评价。

Marco Eugenio, Sousa Patricia, Janoudi Tusneem, de Dreuzy Edouard, Heath Jack M, Viswanathan Ramya, Zuris John A, Gotta Gregory M, Giannoukos Georgia, Hansen Scott, Wood David K, Walters Mark C, Tisdale John F, Wilson Christopher J, Chang Kai-Hsin

Gene Therapy for Sickle Cell Disease: Practice Recommendations from the American Society for Transplantation and Cellular Therapy and the International Society for Cell & Gene Therapy

镰状细胞病基因治疗:美国移植和细胞治疗学会以及国际细胞和基因治疗学会的实践建议

Sharma, Akshay; Kassim, Adetola; Thompson, Alexis; Williams, David A; Liu, Hien D; Boelens, Jaap J; LaBelle, James L; Tisdale, John; de la Fuente, Josu; Kanter, Julie; Krishnamurti, Lakshmanan; Pecker, Lydia H; Walters, Mark C; Eapen, Mary; Porteus, Matt; Bhatia, Monica; Soni, Sandeep; Corbacioglu, Selim; John, Tami D; Cancio, María I

Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells

组合碱基编辑技术将疾病矫正与造血干细胞和祖细胞的谱系扩增相结合

Jia, Kun; Soupene, Eric; Sinha, Roshani; Lesch, Benjamin J; Pendergast, Michael A; Choi, Rachel; Zhang, Xinyi; Foppiani, Elisabetta M; Kostamo, Zachary; Chu, Simon N; Sharma, Devesh; Yu, Xinjie; Cordero, Marco; Walters, Mark C; MacKenzie, Tippi C; Sheehan, Vivien A; Cromer, M Kyle

Targeting FKBP51 prevents stress-induced preterm birth.

靶向FKBP51可预防应激诱发的早产

Guzeloglu-Kayisli Ozlem, Ozmen Asli, Un Busra Cetinkaya, Un Burak, Blas Jacqueline, Johnson Isabella, Thurman Andrea, Walters Mark, Friend David, Kayisli Umit A, Lockwood Charles J

Hematopoietic cell transplant compared with standard care in adolescents and young adults with sickle cell disease

造血干细胞移植与镰状细胞病青少年和青年患者的标准治疗比较

Walters, Mark C; Eapen, Mary; Liu, Yiwen; El Rassi, Fuad; Waller, Edmund K; Levine, John E; Strouse, John J; Antin, Joseph H; Parikh, Suhag H; Bakshi, Nitya; Dampier, Carlton; Jaroscak, Jennifer J; Bergmann, Shayla; Wong, Trisha; Kota, Vamsi; Pace, Betty; Lekakis, Lazaros J; Lulla, Premal; Nickel, Robert S; Kasow, Kimberly A; Popat, Uday; Smith, Wally; Yu, Lolie; DiFronzo, Nancy; Geller, Nancy; Kamani, Naynesh; Klings, Elizabeth S; Hassell, Kathryn; Mendizabal, Adam; Sullivan, Keith; Neuberg, Donna; Krishnamurti, Lakshmanan

Angry and Afraid: Exploring the Impact of Mixed Emotional Reactions to Hate Crimes With LGBT+ and Muslim Communities

愤怒与恐惧:探究LGBT+群体和穆斯林群体对仇恨犯罪的复杂情绪反应的影响

Paterson, Jenny L; Walters, Mark A; Brown, Rupert; Carrasco, Diego

Haploidentical Bone Marrow Transplantation for Sickle Cell Disease

镰状细胞病的单倍体相合骨髓移植

Kassim, Adetola A; Walters, Mark C; Eapen, Mary; Smith, Madoc; Logan, Brent R; Solh, Melhem; McKinney, Christopher; Nieder, Michael; Ross, Maureen; Kent, Michael; Abusin, Ghada A; Mallhi, Kanwaldeep; Silva, Jorge Galvez; Shaughnessy, Paul; Kanter, Julie; Haines, Hilary; Farah, Rafic; Khaled, Yasser A; Ritzau, Nicole; Mendizabal, Adam; Abraham, Allistair; Bollard, Catherine; Cooke, Kenneth; de la Fuente, Josu; Hanna, Rabi; Horowitz, Mary M; Jordan, Lori C; Bakshi, Nitya; Krishnamurti, Lakshmanan; Leifer, Eric; Mahadeo, Kris Michael; Shenoy, Shalini; Jones, Richard J; DeBaun, Michael R; Brodsky, Robert A

Synthesis errors in oligonucleotides are propagated into the genome by homology-directed repair

寡核苷酸合成错误通过同源定向修复机制传播到基因组中。

Wyman, Stacia K; Romero, Zulema; Heo, Seok-Jin; Navarrete, Marian; Krishnappa, Netravathi; Kohn, Donald B; Martin, David Ik; Walters, Mark C; Boffelli, Dario

Long-term outcomes after unrelated donor transplantation for severe sickle cell disease on the BMT CTN 0601 trial

BMT CTN 0601试验中,非亲缘供者移植治疗重度镰状细胞病患者的长期预后

Eapen, Mary; Kou, Jianqun; Andreansky, Martin; Bhatia, Monica; Brochstein, Joel; Chaudhury, Sonali; Haight, Ann E; Haines, Hilary; Jacobsohn, David; Jaroscak, Jennifer; Kasow, Kimberly A; Krishnamurti, Lakshmanan; Levine, John E; Leung, Kathryn; Margolis, David; Yu, Lolie C; Horowitz, Mary M; Kamani, Naynesh; Walters, Mark C; Shenoy, Shalini

Incremental eligibility criteria for the BMT CTN 1507 haploidentical trial for children with sickle cell disease

针对镰状细胞病患儿的 BMT CTN 1507 单倍体相合试验的逐步纳入标准

John, Tami D; Walters, Mark C; Rangarajan, Hemalatha G; Rahim, Mahvish Q; McKinney, Christopher; Bollard, Catherine M; Abusin, Ghada; Eapen, Mary; Kassim, Adetola A; DeBaun, Michael R