日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Nonclinical evaluation of renizgamglogene autogedtemcel for SCD and TDT.

对 renizgamglogene autogedtemcel 治疗 SCD 和 TDT 的非临床评价。

Marco Eugenio, Sousa Patricia, Janoudi Tusneem, de Dreuzy Edouard, Heath Jack M, Viswanathan Ramya, Zuris John A, Gotta Gregory M, Giannoukos Georgia, Hansen Scott, Wood David K, Walters Mark C, Tisdale John F, Wilson Christopher J, Chang Kai-Hsin

Gene Therapy for Sickle Cell Disease: Practice Recommendations from the American Society for Transplantation and Cellular Therapy and the International Society for Cell & Gene Therapy

镰状细胞病基因治疗:美国移植和细胞治疗学会以及国际细胞和基因治疗学会的实践建议

Sharma, Akshay; Kassim, Adetola; Thompson, Alexis; Williams, David A; Liu, Hien D; Boelens, Jaap J; LaBelle, James L; Tisdale, John; de la Fuente, Josu; Kanter, Julie; Krishnamurti, Lakshmanan; Pecker, Lydia H; Walters, Mark C; Eapen, Mary; Porteus, Matt; Bhatia, Monica; Soni, Sandeep; Corbacioglu, Selim; John, Tami D; Cancio, María I

Hematopoietic cell transplant compared with standard care in adolescents and young adults with sickle cell disease

造血干细胞移植与镰状细胞病青少年和青年患者的标准治疗比较

Walters, Mark C; Eapen, Mary; Liu, Yiwen; El Rassi, Fuad; Waller, Edmund K; Levine, John E; Strouse, John J; Antin, Joseph H; Parikh, Suhag H; Bakshi, Nitya; Dampier, Carlton; Jaroscak, Jennifer J; Bergmann, Shayla; Wong, Trisha; Kota, Vamsi; Pace, Betty; Lekakis, Lazaros J; Lulla, Premal; Nickel, Robert S; Kasow, Kimberly A; Popat, Uday; Smith, Wally; Yu, Lolie; DiFronzo, Nancy; Geller, Nancy; Kamani, Naynesh; Klings, Elizabeth S; Hassell, Kathryn; Mendizabal, Adam; Sullivan, Keith; Neuberg, Donna; Krishnamurti, Lakshmanan

Haploidentical Bone Marrow Transplantation for Sickle Cell Disease

镰状细胞病的单倍体相合骨髓移植

Kassim, Adetola A; Walters, Mark C; Eapen, Mary; Smith, Madoc; Logan, Brent R; Solh, Melhem; McKinney, Christopher; Nieder, Michael; Ross, Maureen; Kent, Michael; Abusin, Ghada A; Mallhi, Kanwaldeep; Silva, Jorge Galvez; Shaughnessy, Paul; Kanter, Julie; Haines, Hilary; Farah, Rafic; Khaled, Yasser A; Ritzau, Nicole; Mendizabal, Adam; Abraham, Allistair; Bollard, Catherine; Cooke, Kenneth; de la Fuente, Josu; Hanna, Rabi; Horowitz, Mary M; Jordan, Lori C; Bakshi, Nitya; Krishnamurti, Lakshmanan; Leifer, Eric; Mahadeo, Kris Michael; Shenoy, Shalini; Jones, Richard J; DeBaun, Michael R; Brodsky, Robert A

Synthesis errors in oligonucleotides are propagated into the genome by homology-directed repair

寡核苷酸合成错误通过同源定向修复机制传播到基因组中。

Wyman, Stacia K; Romero, Zulema; Heo, Seok-Jin; Navarrete, Marian; Krishnappa, Netravathi; Kohn, Donald B; Martin, David Ik; Walters, Mark C; Boffelli, Dario

Long-term outcomes after unrelated donor transplantation for severe sickle cell disease on the BMT CTN 0601 trial

BMT CTN 0601试验中,非亲缘供者移植治疗重度镰状细胞病患者的长期预后

Eapen, Mary; Kou, Jianqun; Andreansky, Martin; Bhatia, Monica; Brochstein, Joel; Chaudhury, Sonali; Haight, Ann E; Haines, Hilary; Jacobsohn, David; Jaroscak, Jennifer; Kasow, Kimberly A; Krishnamurti, Lakshmanan; Levine, John E; Leung, Kathryn; Margolis, David; Yu, Lolie C; Horowitz, Mary M; Kamani, Naynesh; Walters, Mark C; Shenoy, Shalini

Incremental eligibility criteria for the BMT CTN 1507 haploidentical trial for children with sickle cell disease

针对镰状细胞病患儿的 BMT CTN 1507 单倍体相合试验的逐步纳入标准

John, Tami D; Walters, Mark C; Rangarajan, Hemalatha G; Rahim, Mahvish Q; McKinney, Christopher; Bollard, Catherine M; Abusin, Ghada; Eapen, Mary; Kassim, Adetola A; DeBaun, Michael R

Neurocognitive outcome in children with sickle cell disease after myeloimmunoablative conditioning and haploidentical hematopoietic stem cell transplantation: a non-randomized clinical trial

镰状细胞病患儿接受骨髓免疫清除预处理和单倍体造血干细胞移植后的神经认知结局:一项非随机临床试验

Braniecki, Suzanne; Vichinsky, Elliott; Walters, Mark C; Shenoy, Shalini; Shi, Qiuhu; Moore, Theodore B; Talano, Julie-An; Parsons, Susan K; Flower, Allyson; Panarella, Anne; Fabricatore, Sandra; Morris, Erin; Mahanti, Harshini; Milner, Jordan; McKinstry, Robert C; Duncan, Christine N; van de Ven, Carmella; Cairo, Mitchell S

Secondary Neoplasms After Hematopoietic Cell Transplant for Sickle Cell Disease

镰状细胞病造血干细胞移植后的继发性肿瘤

Eapen, Mary; Brazauskas, Ruta; Williams, David A; Walters, Mark C; St Martin, Andrew; Jacobs, Benjamin L; Antin, Joseph H; Bona, Kira; Chaudhury, Sonali; Coleman-Cowger, Victoria H; DiFronzo, Nancy L; Esrick, Erica B; Field, Joshua J; Fitzhugh, Courtney D; Kanter, Julie; Kapoor, Neena; Kohn, Donald B; Krishnamurti, Lakshmanan; London, Wendy B; Pulsipher, Michael A; Talib, Sohel; Thompson, Alexis A; Waller, Edmund K; Wun, Ted; Horowitz, Mary M

Lovo-cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB-206 study

Lovo-cel基因疗法治疗镰状细胞病:HGB-206研究初期组的治疗过程演变和结果

Kanter, Julie; Thompson, Alexis A; Pierciey, Francis J Jr; Hsieh, Matthew; Uchida, Naoya; Leboulch, Philippe; Schmidt, Manfred; Bonner, Melissa; Guo, Ruiting; Miller, Alex; Ribeil, Jean-Antoine; Davidson, David; Asmal, Mohammed; Walters, Mark C; Tisdale, John F