日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial.

AAV基因疗法治疗杜氏肌营养不良症:EMBARK 3期随机试验

Mendell Jerry R, Muntoni Francesco, McDonald Craig M, Mercuri Eugenio M, Ciafaloni Emma, Komaki Hirofumi, Leon-Astudillo Carmen, Nascimento Andrés, Proud Crystal, Schara-Schmidt Ulrike, Veerapandiyan Aravindhan, Zaidman Craig M, Guridi Maitea, Murphy Alexander P, Reid Carol, Wandel Christoph, Asher Damon R, Darton Eddie, Mason Stefanie, Potter Rachael A, Singh Teji, Zhang Wenfei, Fontoura Paulo, Elkins Jacob S, Rodino-Klapac Louise R

Immunologic investigations into transgene directed immune-mediated myositis following delandistrogene moxeparvovec gene therapy

对接受 delandistrogene moxeparvovec 基因治疗后发生的转基因导向免疫介导性肌炎进行免疫学研究

Potter, Rachael A; Moeller, Ida H; Khan, Sohrab; Haegel, Hélène; Hollenstein, Andreas; Steiner, Guido; Wandel, Christoph; Murphy, Alexander P; Asher, Damon R; Palatinsky, Emanuel; Griffin, Danielle A; Mason, Stefanie; Iannaccone, Susan T; Zaidman, Craig M; Rodino-Klapac, Louise R

Balovaptan vs Placebo for Social Communication in Childhood Autism Spectrum Disorder: A Randomized Clinical Trial

巴洛伐坦与安慰剂治疗儿童自闭症谱系障碍社交沟通障碍的随机临床试验

Hollander, Eric; Jacob, Suma; Jou, Roger; McNamara, Nora; Sikich, Linmarie; Tobe, Russell; Smith, Janice; Sanders, Kevin; Squassante, Lisa; Murtagh, Lorraine; Gleissl, Teresa; Wandel, Christoph; Veenstra-VanderWeele, Jeremy

A randomized, double-blind, placebo-controlled phase II trial to explore the effects of a GABA(A)-α5 NAM (basmisanil) on intellectual disability associated with Down syndrome

一项随机、双盲、安慰剂对照的II期临床试验,旨在探索GABA(A)-α5 NAM(巴斯米沙尼)对唐氏综合征相关智力障碍的影响。

Goeldner, Celia; Kishnani, Priya S; Skotko, Brian G; Casero, Julian Lirio; Hipp, Joerg F; Derks, Michael; Hernandez, Maria-Clemencia; Khwaja, Omar; Lennon-Chrimes, Sian; Noeldeke, Jana; Pellicer, Sabine; Squassante, Lisa; Visootsak, Jeannie; Wandel, Christoph; Fontoura, Paulo; d'Ardhuy, Xavier Liogier

Erratum to: Clinical trial considerations on male contraception and collection of pregnancy information from female partner: update

勘误:关于男性避孕和收集女性伴侣妊娠信息的临床试验注意事项:更新

Banholzer, Maria Longauer; Wandel, Christoph; Barrow, Paul; Mannino, Marie; Schmitt, Georg; Guérard, Melanie; Müller, Lutz; Greig, Gerard; Amemiya, Kenjie; Peck, Richard; Singer, Thomas; Doessegger, Lucette

Clinical trial considerations on male contraception and collection of pregnancy information from female partner: update

关于男性避孕和收集女性伴侣妊娠信息的临床试验注意事项:最新进展

Banholzer, Maria Longauer; Wandel, Christoph; Barrow, Paul; Mannino, Marie; Schmitt, Georg; Guérard, Melanie; Müller, Lutz; Greig, Gerard; Amemiya, Kenjie; Peck, Richard; Singer, Thomas; Doessegger, Lucette

Clinical trial considerations on male contraception and collection of pregnancy information from female partners

关于男性避孕和收集女性伴侣妊娠信息的临床试验注意事项

Banholzer, Maria Longauer; Buergin, Heinrich; Wandel, Christoph; Schmitt, Georg; Gocke, Elmar; Peck, Richard; Singer, Thomas; Reynolds, Theresa; Mannino, Marie; Deutsch, Jonathan; Doessegger, Lucette