Intra-arterial transplantation of autologous mesoangioblasts in m.3243A>G mutation carriers is safe: First phase 1/2 human clinical study.
对 m.3243A>G 突变携带者进行自体间充质血管母细胞动脉内移植是安全的:第一项 1/2 期人体临床研究。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.07.005
van Tienen Florence H J, Hoeijmakers Janneke G J, van der Leij Christiaan, Timmer Erika, Wanders Nikki, Lindsey Patrick J, Yi Fangzheng, Lin Fong, Kortekaas Susanne P M, Roelofs Helene, Westra Inge M, Meij Pauline, Wijnen Lambert A C M, de Coo Irenaeus F M, Smeets Hubert J M