CRISPR-Cas Genome Editing in Ex Vivo Human Lungs to Rewire the Translational Path of Genome-Targeting Therapeutics.
利用 CRISPR-Cas 基因编辑技术在离体人肺中重塑基因组靶向治疗的转化路径
期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2023.223
Mesaki Kumi, Yamamoto Haruchika, Juvet Stephen, Yeung Jonathan, Guan Zehong, Akhter Akhi, Yao Yan, Dickie Cameron, Mangat Henna, Wang Aizhou, Wilson Gavin W, Mariscal Andrea, Hu Jim, Davidson Alan R, Kleinstiver Benjamin P, Cypel Marcelo, Liu Mingyao, Keshavjee Shaf