Correction of human nonsense mutation via adenine base editing for Duchenne muscular dystrophy treatment in mouse
通过腺嘌呤碱基编辑纠正人类无义突变以治疗小鼠杜氏肌营养不良症
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2024.102165
Ming Jin, Jiajia Lin, Haisen Li, Zhifang Li, Dong Yang, Yin Wang, Yuyang Yu, Zhurui Shao, Long Chen, Zhiqiang Wang, Yu Zhang, Xiumei Zhang, Ning Wang, Chunlong Xu, Hui Yang, Wan-Jin Chen, Guoling Li