Targeted AAV6 gene therapy restores corneal endothelial function in three hereditary corneal dystrophies.
靶向 AAV6 基因疗法可恢复三种遗传性角膜营养不良症患者的角膜内皮功能。
期刊:Cell Reports Medicine
影响因子:10.6
doi:10.1016/j.xcrm.2026.102649
Zhang Bi Ning, Qi Benxiang, Chen Shijiu, Su Jing, Li Guoyun, Wang Xinping, Ren Zhongmei, Zhang Hengrui, Cheng Jun, Qu Jingyu, Yang Yang, Zhou Qingjun, Cong Lin, Xie Lixin