CRISPR activation of the ribosome-associated quality control factor ASCC3 ameliorates fragile X syndrome phenotypes in mice
CRISPR激活核糖体相关质量控制因子ASCC3可改善小鼠脆性X综合征表型
期刊:Science Translational Medicine
影响因子:14.6
doi:10.1126/scitranslmed.adq3551
Geng, Ji; Wang, Xiying; Pan, Jie; Khan, Danish; Pimcharoen, Sopida; Zhang, Yongjie; Mosammaparast, Nima; Hirose, Susumu; Petrucelli, Leonard; Brandman, Onn; Qi, Lei S; Lu, Bingwei