Life-Saving Treatments for Spinal Muscular Atrophy: Global Access and Availability
脊髓性肌萎缩症的救命疗法:全球可及性和可用性
期刊:Neurology-Clinical Practice
影响因子:3.2
doi:10.1212/CPJ.0000000000200224
Armengol, Victor D; Darras, Basil T; Abulaban, Ahmad A; Alshehri, Ali; Barisic, Nina; Ben-Omran, Tawfeg; Bernert, Guenther; Castiglioni, Claudia; Chien, Yin-Hsiu; Farrar, Michelle A; Kandawasvika, Gwendoline; Khadilkar, Satish; Mah, Jean; Marini-Bettolo, Chiara; Osredkar, Damjan; Pfeffer, Gerald; Piazzon, Flavia B; Pitarch Castellano, Inmaculada; Quijano-Roy, Susana; Saito, Kayoko; Shin, Jin-Hong; Vázquez-Costa, Juan F; Walter, Maggie C; Wanigasinghe, Jithangi; Xiong, Hui; Griggs, Robert C; Roy, Bhaskar