Small-molecule activation of lysosomal TRP channels ameliorates Duchenne muscular dystrophy in mouse models
小分子激活溶酶体 TRP 通道可改善小鼠模型中的杜氏肌营养不良症
期刊:Science Advances
影响因子:11.7
doi:10.1126/sciadv.aaz2736
Lu Yu, Xiaoli Zhang, Yexin Yang, Dan Li, Kaiyuan Tang, Zifan Zhao, Wanwan He, Ce Wang, Nirakar Sahoo, Kimber Converso-Baran, Carol S Davis, Susan V Brooks, Anne Bigot, Raul Calvo, Natalia J Martinez, Noel Southall, Xin Hu, Juan Marugan, Marc Ferrer, Haoxing Xu