日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Phase 2 trial of a DNA vaccine (pTVG-HP) and nivolumab in patients with castration-sensitive non-metastatic (M0) prostate cancer

一项针对去势敏感性非转移性(M0)前列腺癌患者的DNA疫苗(pTVG-HP)联合纳武利尤单抗的II期临床试验

McNeel, Douglas G; Emamekhoo, Hamid; Eickhoff, Jens C; Kyriakopoulos, Christos E; Wargowski, Ellen; Tonelli, Tommaso P; Johnson, Laura E; Liu, Glenn

Phase 2 trial of T-cell activation using MVI-816 and pembrolizumab in patients with metastatic, castration-resistant prostate cancer (mCRPC)

使用 MVI-816 和帕博利珠单抗激活 T 细胞治疗转移性去势抵抗性前列腺癌 (mCRPC) 患者的 II 期试验

McNeel, Douglas G; Eickhoff, Jens C; Wargowski, Ellen; Johnson, Laura E; Kyriakopoulos, Christos E; Emamekhoo, Hamid; Lang, Joshua M; Brennan, Mary Jane; Liu, Glenn

Defining the genotypic and phenotypic spectrum of X-linked MSL3-related disorder

明确X连锁MSL3相关疾病的基因型和表型谱

Brunet, Theresa; McWalter, Kirsty; Mayerhanser, Katharina; Anbouba, Grace M; Armstrong-Javors, Amy; Bader, Ingrid; Baugh, Evan; Begtrup, Amber; Bupp, Caleb P; Callewaert, Bert L; Cereda, Anna; Cousin, Margot A; Del Rey Jimenez, Juan C; Demmer, Laurie; Dsouza, Nikita R; Fleischer, Nicole; Gavrilova, Ralitza H; Ghate, Sumedha; Graf, Elisabeth; Green, Andrew; Green, Sarah R; Iascone, Maria; Kdissa, Ameni; Klee, Dirk; Klee, Eric W; Lancaster, Emily; Lindstrom, Kristin; Mayr, Johannes A; McEntagart, Meriel; Meeks, Naomi J L; Mittag, Dana; Moore, Harrison; Olsen, Anne K; Ortiz, Damara; Parsons, Gretchen; Pena, Loren D M; Person, Richard E; Punj, Sumit; Ramos-Rivera, Gonzalo Alonso; Sacoto, Maria J Guillen; Bradley Schaefer, G; Schnur, Rhonda E; Scott, Tiana M; Scott, Daryl A; Serbinski, Carolyn R; Shashi, Vandana; Siu, Victoria M; Stadheim, Barbro Fossøy; Sullivan, Jennifer A; Švantnerová, Jana; Velsher, Lea; Wargowski, David S; Wentzensen, Ingrid M; Wieczorek, Dagmar; Winkelmann, Juliane; Yap, Patrick; Zech, Michael; Zimmermann, Michael T; Meitinger, Thomas; Distelmaier, Felix; Wagner, Matias

Alternative genomic diagnoses for individuals with a clinical diagnosis of Dubowitz syndrome

针对临床诊断为杜博维茨综合征患者的替代基因组诊断方法

Dyment, David A; O'Donnell-Luria, Anne; Agrawal, Pankaj B; Coban Akdemir, Zeynep; Aleck, Kyrieckos A; Antaki, Danny; Al Sharhan, Hind; Au, Ping-Yee B; Aydin, Hatip; Beggs, Alan H; Bilguvar, Kaya; Boerwinkle, Eric; Brand, Harrison; Brownstein, Catherine A; Buyske, Steve; Chodirker, Bernard; Choi, Jungmin; Chudley, Albert E; Clericuzio, Carol L; Cox, Gerald F; Curry, Cynthia; de Boer, Elke; de Vries, Bert B A; Dunn, Kathryn; Dutmer, Cullen M; England, Eleina M; Fahrner, Jill A; Geckinli, Bilgen B; Genetti, Casie A; Gezdirici, Alper; Gibson, William T; Gleeson, Joseph G; Greenberg, Cheryl R; Hall, April; Hamosh, Ada; Hartley, Taila; Jhangiani, Shalini N; Karaca, Ender; Kernohan, Kristin; Lauzon, Julie L; Lewis, M E Suzanne; Lowry, R Brian; López-Giráldez, Francesc; Matise, Tara C; McEvoy-Venneri, Jennifer; McInnes, Brenda; Mhanni, Aziz; Garcia Minaur, Sixto; Moilanen, Jukka; Nguyen, An; Nowaczyk, Malgorzata J M; Posey, Jennifer E; Õunap, Katrin; Pehlivan, Davut; Pajusalu, Sander; Penney, Lynette S; Poterba, Timothy; Prontera, Paolo; Doriqui, Maria Juliana Rodovalho; Sawyer, Sarah L; Sobreira, Nara; Stanley, Valentina; Torun, Deniz; Wargowski, David; Witmer, P Dane; Wong, Isaac; Xing, Jinchuan; Zaki, Maha S; Zhang, Yeting; Boycott, Kym M; Bamshad, Michael J; Nickerson, Deborah A; Blue, Elizabeth E; Innes, A Micheil

Multicenter Phase I Trial of a DNA Vaccine Encoding the Androgen Receptor Ligand-binding Domain (pTVG-AR, MVI-118) in Patients with Metastatic Prostate Cancer

一项针对转移性前列腺癌患者的多中心 I 期临床试验,研究编码雄激素受体配体结合域的 DNA 疫苗(pTVG-AR,MVI-118)的疗效

Kyriakopoulos, Christos E; Eickhoff, Jens C; Ferrari, Anna C; Schweizer, Michael T; Wargowski, Ellen; Olson, Brian M; McNeel, Douglas G

Treatment Combinations with DNA Vaccines for the Treatment of Metastatic Castration-Resistant Prostate Cancer (mCRPC)

DNA疫苗联合治疗转移性去势抵抗性前列腺癌(mCRPC)

Gamat-Huber, Melissa; Jeon, Donghwan; Johnson, Laura E; Moseman, Jena E; Muralidhar, Anusha; Potluri, Hemanth K; Rastogi, Ichwaku; Wargowski, Ellen; Zahm, Christopher D; McNeel, Douglas G

Phase II Trial of a DNA Vaccine Encoding Prostatic Acid Phosphatase (pTVG-HP [MVI-816]) in Patients With Progressive, Nonmetastatic, Castration-Sensitive Prostate Cancer

一项针对进展性、非转移性、去势敏感性前列腺癌患者的编码前列腺酸性磷酸酶的DNA疫苗(pTVG-HP [MVI-816])的II期临床试验

McNeel, Douglas G; Eickhoff, Jens C; Johnson, Laura E; Roth, Alison R; Perk, Timothy G; Fong, Lawrence; Antonarakis, Emmanuel S; Wargowski, Ellen; Jeraj, Robert; Liu, Glenn

Prime-boost vaccination targeting prostatic acid phosphatase (PAP) in patients with metastatic castration-resistant prostate cancer (mCRPC) using Sipuleucel-T and a DNA vaccine

在转移性去势抵抗性前列腺癌 (mCRPC) 患者中,采用 Sipuleucel-T 和 DNA 疫苗进行针对前列腺酸性磷酸酶 (PAP) 的初免-加强免疫接种。

Wargowski, Ellen; Johnson, Laura E; Eickhoff, Jens C; Delmastro, Lauren; Staab, Mary Jane; Liu, Glenn; McNeel, Douglas G

Concurrent, but not sequential, PD-1 blockade with a DNA vaccine elicits anti-tumor responses in patients with metastatic, castration-resistant prostate cancer

同时(而非先后)使用 PD-1 阻断剂和 DNA 疫苗可诱导转移性去势抵抗性前列腺癌患者产生抗肿瘤反应。

McNeel, Douglas G; Eickhoff, Jens C; Wargowski, Ellen; Zahm, Christopher; Staab, Mary Jane; Straus, Jane; Liu, Glenn

Mutations in RAB39B cause X-linked intellectual disability and early-onset Parkinson disease with α-synuclein pathology

RAB39B 突变可导致 X 连锁智力障碍和伴有 α-突触核蛋白病理的早发性帕金森病

Gabrielle R Wilson, Joe C H Sim, Catriona McLean, Maila Giannandrea, Charles A Galea, Jessica R Riseley, Sarah E M Stephenson, Elizabeth Fitzpatrick, Stefan A Haas, Kate Pope, Kirk J Hogan, Ronald G Gregg, Catherine J Bromhead, David S Wargowski, Christopher H Lawrence, Paul A James, Andrew Churchya