Long-term CSF responses in adult patients with spinal muscular atrophy type 2 or 3 on treatment with nusinersen
接受诺西那生治疗的2型或3型脊髓性肌萎缩症成年患者的长期脑脊液反应
期刊:Journal of Neurology
影响因子:4.6
doi:10.1007/s00415-025-12984-7
Cebulla, Gina; Hai, Ling; Warnken, Uwe; Güngör, Cansu; Hoffmann, Dirk C; Korporal-Kuhnke, Mirjam; Wildemann, Brigitte; Wick, Wolfgang; Kessler, Tobias; Weiler, Markus