Modified AAV5 capsid for improved brain biodistribution following direct injection in preclinical models.
改良的 AAV5 衣壳可在临床前模型中直接注射后改善脑部生物分布。
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101642
Kieper Sebastian N, Spronck Elisabeth A, Bourajjaj Meriem, Morais Roberto D V S, van der Bent M Leontien, Acar Broekmans Seyda, van Rooijen Charlot, van Westen Rhodé, Squeri Giorgia, Brasser Giso, Wartel Morgane, Waaijer Stijn J H, Hoornenborg C Warner, Hoogland Tycho M, Porter Richard, Anggakusuma