Cas9-specific immune responses compromise local and systemic AAV CRISPR therapy in multiple dystrophic canine models
Cas9 特异性免疫反应影响多种营养不良犬模型中的局部和全身 AAV CRISPR 疗法
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-021-26830-7
Chady H Hakim, Sandeep R P Kumar #, Dennis O Pérez-López #, Nalinda B Wasala, Dong Zhang, Yongping Yue, James Teixeira, Xiufang Pan, Keqing Zhang, Emily D Million, Christopher E Nelson, Samantha Metzger, Jin Han, Jacqueline A Louderman, Florian Schmidt, Feng Feng, Dirk Grimm, Bruce F Smith, Gang Yao