日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophy

利司他林治疗并未导致脊髓性肌萎缩症患者出现视网膜毒性。

Sergott, Robert C; Amorelli, Giulia M; Baranello, Giovanni; Barreau, Emmanuel; Beres, Shannon; Kane, Steven; Mercuri, Eugenio; Orazi, Lorenzo; SantaMaria, Melissa; Tremolada, Gemma; Santarsiero, Diletta; Waskowska, Agnieszka; Yashiro, Shigeko; Denk, Nora; Fürst-Recktenwald, Sabine; Gerber, Marianne; Gorni, Ksenija; Jaber, Birgit; Jacobsen, Bjoern; Mueller, Lutz; Nave, Stephane; Scalco, Renata S; Marzoli, Stefania B