Mitochondria-Homing Drug Mitochonic Acid 5 Improves Barth Syndrome Myopathy in a Human-Induced Pluripotent Stem Cell Model and Barth Syndrome Drosophila Model.
线粒体归巢药物线粒体酸 5 可改善人类诱导多能干细胞模型和巴特综合征果蝇模型中的巴特综合征肌病
期刊:FASEB Journal
影响因子:4.2
doi:10.1096/fj.202401856RRR
Tongu Yoshiyasu, Kasahara Tomoko, Matsuhashi Tetsuro, Oikawa Yoshitsugu, Akimoto Ryota, Luo Yuhan, Sekine Sayaka, Suzuki Momoka, Kashiwagi Hitomi, Kanno Shinichiro, Tanaka Yoshikazu, Sato Kyohei, Okubo Yusuke, Muto Akihiko, Tokuno Hidetaka, Suzuki Chitose, Kawabe Chiharu, Ishikawa Takamasa, Watanabe Shun, Kikuchi Koichi, Itai Shun, Sato Takeya, Suzuki Takehiro, Igarashi Kazuhiro, Fukuda Shinji, Soga Tomoyoshi, Murayama Kei, Kuranaga Erina, Toyohara Takafumi, Abe Takaaki
发育与干细胞
细胞生物学
Drosophila
Human
线粒体