RuvBL1/2 reduce toxic dipeptide repeat protein burden in multiple models of C9orf72-ALS/FTD.
RuvBL1/2 可降低多种 C9orf72-ALS/FTD 模型中的毒性二肽重复蛋白负荷
期刊:Life Science Alliance
影响因子:2.9
doi:10.26508/lsa.202402757
Webster Christopher P, Hall Bradley, Crossley Olivia M, Dauletalina Dana, King Marianne, Lin Ya-Hui, Castelli Lydia M, Yang Zih-Liang, Coldicott Ian, Kyrgiou-Balli Ergita, Higginbottom Adrian, Ferraiuolo Laura, De Vos Kurt J, Hautbergue Guillaume M, Shaw Pamela J, West Ryan Jh, Azzouz Mimoun