日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Design of miniprotein inhibitors targeting complement C9 to block membrane attack complex assembly

设计靶向补体C9的微型蛋白抑制剂以阻断膜攻击复合物的组装

Li, Min; Wang, Ningning; Fu, Xiaoyan; Wei, Gege; Zhang, Ze; Yu, Yanghan; Xue, Tianshui; Zhao, Yifei; Pan, Jinheng; Wang, Dongfeng; Liu, Meifang; Li, Yong; Tang, Jinbao; Cao, Longxing; Jian, Zhaocheng; Liang, Shujuan; Yu, Bowen

Single Administration of AAV-mAtp6v1b2 Gene Therapy Rescues Hearing and Vestibular Disorders Caused by Atp6v1b2-Induced Lysosomal Dysfunction in Hair Cells.

单次注射 AAV-mAtp6v1b2 基因疗法可挽救由 Atp6v1b2 诱导的毛细胞溶酶体功能障碍引起的听力和前庭疾病

Wei Gege, Qiu Shiwei, Gao Xue, Zheng Lu, Chen Yijin, Ma Ying, Feng Haifeng, Yang Jinyuan, Dong Guojie, Nie Huiyi, Zhao Weihao, Li Xiaoge, Wang Guangqin, Xiong Wei, Dai Pu, Yuan Yongyi

Novel autosomal dominant syndromic hearing loss caused by COL4A2 -related basement membrane dysfunction of cochlear capillaries and microcirculation disturbance

一种由COL4A2相关基底膜功能障碍引起的耳蜗毛细血管和微循环紊乱导致的新型常染色体显性遗传综合征性听力损失。

Yang, Jinyuan; Ma, Ying; Gao, Xue; Qiu, Shiwei; Li, Xiaoge; Zhao, Weihao; Chen, Yijin; Dong, Guojie; Lin, Rongfeng; Wei, Gege; Nie, Huiyi; Feng, Haifeng; Gu, Xiaoning; Gao, Bo; Dai, Pu; Yuan, Yongyi