日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

In Memoriam: Alberto Piazza (1941–2024)

悼念:阿尔贝托·皮亚扎 (1941–2024)

Ku, Cristy A; Wei, Lisa W; Sieving, Paul A; Matullo, Giuseppe; Amoroso, Antonio

Xist-mediated silencing requires additive functions of SPEN and Polycomb together with differentiation-dependent recruitment of SmcHD1

Xist介导的沉默需要SPEN和Polycomb的协同作用,以及SmcHD1的分化依赖性募集。

Joseph S Bowness ,Tatyana B Nesterova ,Guifeng Wei ,Lisa Rodermund ,Mafalda Almeida ,Heather Coker ,Emma J Carter ,Artun Kadaster ,Neil Brockdorff

Immune function in X-linked retinoschisis subjects in an AAV8-RS1 phase I/IIa gene therapy trial

在AAV8-RS1 I/IIa期基因治疗试验中,X连锁视网膜劈裂症患者的免疫功能

Mishra, Alaknanda; Vijayasarathy, Camasamudram; Cukras, Catherine A; Wiley, Henry E; Sen, H Nida; Zeng, Yong; Wei, Lisa L; Sieving, Paul A

CBFB-MYH11 fusion transcripts distinguish acute myeloid leukemias with distinct molecular landscapes and outcomes

CBFB-MYH11融合转录本可区分具有不同分子特征和预后的急性髓系白血病。

Huang, Benjamin J; Smith, Jenny L; Wang, Yi-Cheng; Taghizadeh, Kassra; Leonti, Amanda R; Ries, Rhonda E; Liu, Yanling; Kolekar, Pandurang; Tarlock, Katherine; Gerbing, Robert; Crowgey, Erin; Furlan, Scott N; Shaw, Timothy I; Hagiwara, Kohei; Wei, Lisa; Cooper, Todd M; Gamis, Alan S; Aplenc, Richard; Kolb, E Anders; Farrar, Jason E; Triche, Timothy; Alonzo, Todd A; Ma, Xiaotu; Meshinchi, Soheil

Remodeling of the m6A landscape in the heart reveals few conserved post-transcriptional events underlying cardiomyocyte hypertrophy

心脏中 m6A 景观的重塑揭示了心肌细胞肥大背后的一些保守的转录后事件

Scott A Hinger, Jiangbo Wei, Lisa E Dorn, Bryan A Whitson, Paul M L Janssen, Chuan He, Federica Accornero

Trans-Ocular Electric Current In Vivo Enhances AAV-Mediated Retinal Transduction in Large Animal Eye After Intravitreal Vector Administration

体内经眼电刺激可增强玻璃体内注射AAV载体后大动物眼内视网膜的AAV介导转导。

Song, Hongman; Zeng, Yong; Sardar Pasha, Sheik Pran Babu; Bush, Ronald A; Vijayasarathy, Camasamudram; Qian, Haohua; Wei, Lisa; Wiley, Henry E; Wu, Zhijian; Sieving, Paul A

Identification and Analyses of Extra-Cranial and Cranial Rhabdoid Tumor Molecular Subgroups Reveal Tumors with Cytotoxic T Cell Infiltration.

颅外和颅内横纹肌样瘤分子亚组的鉴定和分析揭示了具有细胞毒性 T 细胞浸润的肿瘤

Chun Hye-Jung E, Johann Pascal D, Milne Katy, Zapatka Marc, Buellesbach Annette, Ishaque Naveed, Iskar Murat, Erkek Serap, Wei Lisa, Tessier-Cloutier Basile, Lever Jake, Titmuss Emma, Topham James T, Bowlby Reanne, Chuah Eric, Mungall Karen L, Ma Yussanne, Mungall Andrew J, Moore Richard A, Taylor Michael D, Gerhard Daniela S, Jones Steven J M, Korshunov Andrey, Gessler Manfred, Kerl Kornelius, Hasselblatt Martin, Frühwald Michael C, Perlman Elizabeth J, Nelson Brad H, Pfister Stefan M, Marra Marco A, Kool Marcel

Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery

用于治疗X连锁视网膜劈裂症的视网膜AAV8-RS1基因疗法:玻璃体内注射I/IIa期临床试验的初步结果

Cukras, Catherine; Wiley, Henry E; Jeffrey, Brett G; Sen, H Nida; Turriff, Amy; Zeng, Yong; Vijayasarathy, Camasamudram; Marangoni, Dario; Ziccardi, Lucia; Kjellstrom, Sten; Park, Tae Kwon; Hiriyanna, Suja; Wright, J Fraser; Colosi, Peter; Wu, Zhijian; Bush, Ronald A; Wei, Lisa L; Sieving, Paul A

Convergence of Human Genetics and Animal Studies: Gene Therapy for X-Linked Retinoschisis

人类遗传学与动物研究的融合:X连锁视网膜劈裂症的基因治疗

Bush, Ronald A; Wei, Lisa L; Sieving, Paul A

Ocular localization and transduction by adenoviral vectors are serotype-dependent and can be modified by inclusion of RGD fiber modifications

腺病毒载体的眼部定位和转导取决于血清型,并且可以通过引入RGD纤维修饰进行改变。

Ueyama, Kazuhiro; Mori, Keisuke; Shoji, Takuhei; Omata, Hidekazu; Gehlbach, Peter L; Brough, Douglas E; Wei, Lisa L; Yoneya, Shin