日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Phase 1 pilot study for hemophilia-A: AAV8 vector with prophylactic tacrolimus-glucocorticoid achieves therapeutic FVIII activity

针对A型血友病的I期试点研究:AAV8载体联合预防性他克莫司-糖皮质激素治疗可达到治疗性FVIII活性。

Liu, Wei; Pei, Xiaolei; Yu, Tenghui; Xu, Bingqi; Dai, Xinyue; Xue, Feng; Chen, Lingling; Wang, Xiaolin; Wang, Yuhua; Chen, Yunfei; Liu, Xiaofan; Fu, Rongfeng; Wang, Wentian; Chi, Ying; Li, Hui Yuan; Yang, Renchi; Zhang, Lei

Author Correction: Defective DNA damage repair leads to frequent catastrophic genomic events in murine and human tumors

作者更正:DNA损伤修复缺陷会导致小鼠和人类肿瘤中频繁发生灾难性的基因组事件。

Ratnaparkhe, Manasi; Wong, John K L; Wei, Pei-Chi; Hlevnjak, Mario; Kolb, Thorsten; Simovic, Milena; Haag, Daniel; Paul, Yashna; Devens, Frauke; Northcott, Paul; Jones, David T W; Kool, Marcel; Jauch, Anna; Pastorczak, Agata; Mlynarski, Wojciech; Korshunov, Andrey; Kumar, Rajiv; Downing, Susanna M; Pfister, Stefan M; Zapatka, Marc; McKinnon, Peter J; Alt, Frederick W; Lichter, Peter; Ernst, Aurélie

Recurrent DNA break clusters drive replication-stress-induced copy number variants and genome diversification

反复出现的DNA断裂簇驱动复制压力诱导的拷贝数变异和基因组多样化

Corazzi, Lorenzo; Ing, Alex; Benito, Eva; Cosenza, Marco Raffaele; Hasenfeld, Patrick; Weber, Thomas; Marx, Anna J M; Ionasz, Vivien S; Trausch, Nathan; Benedetto, Sarah; Di Muzio, Giulia; Ding, Boyu; Berlanda, Jana; Giaisi, Marco; Claudino, Nina; Höfer, Thomas; Korbel, Jan O; Wei, Pei-Chi

CSF1R T567M mutation induces microglial dysfunction and synaptic impairment in patient iPSC-derived cerebral organoids of CSF1R-related disorder.

CSF1R T567M 突变导致 CSF1R 相关疾病患者的 iPSC 衍生脑类器官中小胶质细胞功能障碍和突触损伤。

Chi Li, Tu Haitao, Li Zhihong, Qiu Lifeng, Zhang Zhi-Wei, Chia Sook-Yoong, Tan Jayne Yi, Ho Ivy A W, Loh Yuin-Han, Tan Eng-King, Teng Wei, Pei Zhong, Wszolek Zbigniew K, Ng Adeline S L, Zeng Li

Preclinical drug screen identifies WEE1 inhibitor and vinca alkaloid as a combination treatment concept for Li-Fraumeni syndrome medulloblastoma.

临床前药物筛选发现 WEE1 抑制剂和长春花生物碱可作为李-弗劳梅尼综合征髓母细胞瘤的联合治疗方案。

Kolodziejczak Anna S, Selt Florian, Peterziel Heike, Jamaladdin Nora, Mack Norman, Maaß Kendra, Meulenbroeks Chris, Sigaud Romain, Herold-Mende Christel, El Damaty Ahmed, Burhenne Jürgen, Ohmura Shunya, Holland-Letz Tim, Kutscher Lena M, Ernst Aurélie, Wei Pei-Chi, Grünewald Thomas G P, Oehme Ina, Kool Marcel, Jones David T W, Pajtler Kristian W, Kratz Christian P, Pfister Stefan M, Witt Olaf, Milde Till

Screening for Clinically Significant Nephrolithiasis Based on Simple Health Checkup Clinical and Urine Parameters in General Populations: Multicenter Machine Learning Study

基于简易健康体检的临床和尿液参数对一般人群进行具有临床意义的肾结石筛查:多中心机器学习研究

Chen, Hao-Wei; Wei, Pei-Siou; Chen, Yu-Chen; Wu, Jeng-Yih; Lin, Chia-I; Chou, Yii-Her; Juan, Yung-Shun; Wu, Wen-Jeng; Kao, Chung-Yao; Lee, Jung-Ting

Endophytic fungi and their secondary metabolites in Qin medicine plants: a comprehensive review of diversity, function, and application

秦药用植物内生真菌及其次生代谢产物:多样性、功能和应用综述

Chen, Bo-Yang; Li, Tong; Shi, Wen-Pu; Yang, Juan-Juan; Bai, Yang; Xue, Qi-Meng; Jiao, Chen-Li; Wei, Pei-Feng; Chen, Liang-Liang

Correlation Between T1 Rho Value of Magnetic Resonance and Clinical Characteristics of Patients with Knee Osteoarthritis and Analysis of Related Factors of T1 Rho Value

磁共振T1ρ值与膝骨关节炎患者临床特征的相关性及T1ρ值相关因素分析

Zhao, Rui; Xu, Kai; Song, Wei; Zhang, Tao; Cao, Wei; Pei, Fang

Organocatalyzed Enantioselective C-N Bond-Forming S(N)Ar Reactions for Synthesizing Stereogenic-at-Boron BODIPYs

有机催化对映选择性CN键形成S(N)Ar反应合成硼立体异构体BODIPY

Meng, Yan-Dong; Fang, Wei; Pei, Zheng-Hao; Chen, Wen-Hao; Ding, Shu-Ying; Shen, Meng-Lan; Bu, Yingcui; Yao, Chuan-Zhi; Li, Qiankun; Yu, Jie; Jiang, Hua-Jie

Micropatterning Photoconductive Peptide Assemblies on Stiff and Soft Biomaterial Substrates

在刚性和柔性生物材料基底上微图案化光导肽组装体

Lundqvist, Emil M; Lee, Kathryn K; Le, Lanie; Nguyen, Krystal; Lim, Sujeung; Celt, Natalie; Kuang, Yuyao; Yao, Ze-Fan; Wu, Haotian; Tang, Sheng Wei; Pei, Jian; Ardoña, Herdeline Ann M