日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Skeletal muscle effects of antisense oligonucleotides targeting glycogen synthase 1 in a mouse model of Pompe disease.

针对庞贝氏病小鼠模型中糖原合成酶 1 的反义寡核苷酸对骨骼肌的影响

Weiss Lan, Carrer Michele, Shmara Alyaa, Martin Angela, Yin Hong, Pal Pallabi, Cheng Cheng, Ta Lac, Boock Victoria, Fazeli Yasamin, Chang Mindy, Paguio Marvin, Lee Jonathan, Yu Howard, Weiss John, Grossman Tamar R, Raben Nina, Jafar-Nejad Paymaan, Kimonis Virginia

Skeletal muscle effects of antisense oligonucleotides targeting glycogen synthase 1 in a mouse model of Pompe disease

在庞贝病小鼠模型中,靶向糖原合成酶1的反义寡核苷酸对骨骼肌的影响

Weiss, Lan; Carrer, Michele; Shmara, Alyaa; Cheng, Cheng; Yin, Hong; Ta, Lac; Boock, Victoria; Fazeli, Yasamin; Chang, Mindy; Paguio, Marvin; Lee, Jonathan; Yu, Howard; Martin, Angela; Raben, Nina; Weiss, John; Grossman, Tamar; Jafar-Nejad, Paymaan; Kimonis, Virginia

Genetic risk for dengue hemorrhagic fever and dengue fever in multiple ancestries

多种族人群罹患登革出血热和登革热的遗传风险

Pare, Guillaume; Neupane, Binod; Eskandarian, Sasha; Harris, Eva; Halstead, Scott; Gresh, Lionel; Kuan, Guillermina; Balmaseda, Angel; Villar, Luis; Rojas, Elsa; Osorio, Jorge E; Anh, Dang Duc; De Silva, Aruna Dharshan; Premawansa, Sunil; Premawansa, Gayani; Wijewickrama, Ananda; Lorenzana, Ivette; Parham, Leda; Rodriguez, Cynthia; Fernandez-Salas, Ildefonso; Sanchez-Casas, Rosa; Diaz-Gonzalez, Esteban E; Saw Aye, Khin; May, Win Lai; Thein, Min; Bucardo, Filemon; Reyes, Yaoska; Blandon, Patricia; Hirayama, Kenji; Weiss, Lan; Singh, Pardeep; Newton, Jennifer; Loeb, Mark

Kinetics of CD4(+) T Helper and CD8(+) Effector T Cell Responses in Acute Dengue Patients

登革热急性期患者CD4(+)辅助性T细胞和CD8(+)效应性T细胞反应的动力学

Manh, Dao Huy; Weiss, Lan Nguyen; Thuong, Nguyen Van; Mizukami, Shusaku; Dumre, Shyam Prakash; Luong, Quang Chan; Thanh, Le Chi; Thang, Cao Minh; Huu, Pham Thanh; Phuc, Le Hong; Nhung, Cao Thi Hong; Mai, Nguyen Thi; Truong, Nguyen Quang; Ngu, Vu Thien Thu; Quoc, Do Kien; Ha, Tran Thi Ngoc; Ton, Tran; An, Tran Van; Halhouli, Oday; Quynh, Le Nhat; Kamel, Mohamed Gomaa; Karbwang, Juntra; Huong, Vu Thi Que; Huy, Nguyen Tien; Hirayama, Kenji

Plasma cell-free DNA: a potential biomarker for early prediction of severe dengue

血浆游离DNA:一种用于早期预测重症登革热的潜在生物标志物

Phuong, Nguyen Thi Ngoc; Manh, Dao Huy; Dumre, Shyam Prakash; Mizukami, Shusaku; Weiss, Lan Nguyen; Van Thuong, Nguyen; Ha, Tran Thi Ngoc; Phuc, Le Hong; Van An, Tran; Tieu, Thuan Minh; Kamel, Mohamed Gomaa; Morra, Mostafa Ebraheem; Huong, Vu Thi Que; Huy, Nguyen Tien; Hirayama, Kenji

Newborn screening for Prader-Willi syndrome is feasible: Early diagnosis for better outcomes

新生儿普拉德-威利综合征筛查是可行的:早期诊断可带来更好的预后

Mahmoud, Ranim; Singh, Preeti; Weiss, Lan; Lakatos, Anita; Oakes, Melanie; Hossain, Waheeda; Butler, Merlin G; Kimonis, Virginia