日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Silencing of BCL11A by disrupting enhancer-dependent epigenetic insulation

通过破坏增强子依赖的表观遗传绝缘来沉默 BCL11A

Wang, Kaili; Wang, Juan; Feng, Ruopeng; Dudnyk, Kseniia; Kim, Yoon Jung; Lim, Jun Yi Stanley; Lee, Michael Jr; Zhang, Yuannyu; Gao, Xiaofei; Cheng, Yong; Orkin, Stuart H; Zhou, Jian; Weiss, Mitchell J; Yue, Feng; Xu, Jian

Disrupting epigenetic insulation underlies CRISPR therapy for β-hemoglobinopathies

破坏表观遗传绝缘是CRISPR疗法治疗β-血红蛋白病的基础。

Wang, Kaili; Wang, Juan; Weiss, Mitchell J; Yue, Feng; Xu, Jian

A new advance in therapeutic induction of fetal hemoglobin on an uncertain road to durable access

胎儿血红蛋白治疗诱导技术的新进展,但其能否长期应用仍存在不确定性。

Manwani, Deepa; Capellera-Garcia, Sandra; Weiss, Mitchell J

Single-cell transcriptomics reveals heterocellular γ-globin gene expression in Aγδβ-thalassemia

单细胞转录组学揭示Aγδβ-地中海贫血中异质细胞γ-珠蛋白基因表达。

Doerfler, Phillip A; Li, Yichao; Yao, Yu; Feng, Ruopeng; Mayuranathan, Thiyagaraj; Zhang, Jingjing; Kooienga, Emilia; Cullins, David L; Jesudas, Rohith; Williams, Dillon C; Hankins, Jane S; Cheng, Yong; Wood, David K; Weiss, Mitchell J

Endothelial Cell Secretome Alterations Induced by Inflammatory Stress

炎症应激诱导的内皮细胞分泌组改变

Tang, Vi T; Baid, Srishti; Castellanos, Alejandra; Basrur, Venkatesha; Kretz, Colin A; Nesvizhskii, Alexey I; Gao, Xiang; Dong, Qunfeng; Weiss, Mitchell J; Abbineni, Prabhodh S

Murine hematopoietic progenitor cell lines with erythroid and megakaryocyte potential.

具有红系和巨核系潜能的小鼠造血祖细胞系

Wu Ruiqiong, Salehi Faraz, Redecke Vanessa, Ma Zhijun, Marchetti Marco, Finkelstein David, Xu Peng, Cheng Yong, Queisser Kimberly A, Petrey Aaron C, Field Conroy O, Ahn Hyun Sook, Poncz Mortimer, Weiss Mitchell J, Häcker Hans

Engraftment and persistence of HBB base-edited hematopoietic stem cells in nonhuman primates

HBB碱基编辑的造血干细胞在非人灵长类动物中的植入和持久性

Radtke, Stefan; Fields, Emily; Swing, Kyle; Kanestrom, Greta; Yen, Jonathan S; Pande, Dnyanada; Enstrom, Mark R; Humbert, Olivier; Weiss, Mitchell J; Liu, David R; Newby, Gregory A; Kiem, Hans-Peter

Corrigendum to STAT1 promotes megakaryopoiesis downstream of GATA-1 in mice

更正:STAT1 在小鼠中通过 GATA-1 下游途径促进巨核细胞生成

Huang, Zan; Richmond, Terri D; Muntean, Andrew G; Barber, Dwayne L; Weiss, Mitchell J; Crispino, John D

Preclinical development of lentiviral vector gene therapy for Diamond-Blackfan anemia syndrome.

针对Diamond-Blackfan贫血综合征的慢病毒载体基因疗法的临床前开发

Bhoopalan Senthil Velan, Mayuranathan Thiyagaraj, Liu Nana, Mayberry Kalin, Yao Yu, Zhang Jingjing, Métais Jean-Yves, Yan Koon-Kiu, Throm Robert E, Ellis Steven R, Ju Yan, Han Lei, Suryaprakash Shruthi, Palmer Lance E, Zhou Sheng, Yu Jiyang, Cheng Yong, Yen Jonathan S, Gottschalk Stephen, Weiss Mitchell J

KDIGO-defined kidney dysfunction predicts long-term outcomes in a multicenter cohort of adults with sickle cell disease

KDIGO定义的肾功能障碍可预测镰状细胞病成人患者的多中心队列研究的长期预后

Zhang, Xu; DeBaun, Michael R; Wuichet, Kristin; Zahr, Rima; Ivy, Zalaya; Weiss, Mitchell J; Bick, Alex G; Gordeuk, Victor R; Saraf, Santosh L