Small interfering RNA-mediated allele-selective silencing of von Willebrand factor in vitro and in vivo
小干扰 RNA 介导的体内外血管性血友病因子等位基因选择性沉默
期刊:Blood Advances
影响因子:7.4
doi:10.1182/bloodadvances.2023010643
Yvonne K Jongejan, Elisa Schrader Echeverri, Richard J Dirven, Kalina Paunovska, Noa A Linthorst, Annika de Jong, Johannes C Wellershoff, Kim D van der Gouw, Bart J M van Vlijmen, James E Dahlman, Jeroen C J Eikenboom