A charitable access program for patients with lysosomal storage disorders in underserved communities worldwide
一项面向全球服务不足社区溶酶体贮积症患者的慈善援助项目
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-020-01645-9
Mehta, Atul; Ramaswami, Uma; Muenzer, Joseph; Giugliani, Roberto; Ullrich, Kurt; Collin-Histed, Tanya; Panahloo, Zoya; Wellhoefer, Hartmann; Frader, Joel