In vivo base editing reduces liver cysts in autosomal dominant polycystic kidney disease
体内碱基编辑可减少常染色体显性多囊肾病中的肝囊肿
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.08.026
Ibel, Antonia; Bhardwaj, Rishi; Yilmaz, Duygu Elif; Kong, Shuhan; Wendlinger, Sarah; Cordero, Carlos; Papaioannou, Dimitra; Papazian, Maria; Schönauer, Ria; Meng, Qiyao; Eckardt, Kai-Uwe; Hassan, Fatima; Volpe, Isabel; Klämbt, Verena; Halbritter, Jan; Fedeles, Sorin; Krappitz, Matteus; Kaminski, Michael M