Correction of the pathogenic mutation in TGM1 gene by adenine base editing in mutant embryos
通过腺嘌呤碱基编辑纠正突变胚胎中TGM1基因的致病突变
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2021.05.007
Lu Dang ,Xueliang Zhou ,Xiufang Zhong ,Wenxia Yu ,Shisheng Huang ,Hanyan Liu ,Yuanyuan Chen ,Wuwen Zhang ,Lihua Yuan ,Lei Li ,Xingxu Huang ,Guanglei Li ,Jianqiao Liu ,Guoqing Tong