日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Translating cell therapies for neurodegenerative diseases: Huntington's disease as a model disorder

将细胞疗法应用于神经退行性疾病:以亨廷顿病为例

Rosser, Anne E; Busse, Monica E; Gray, William P; Badin, Romina Aron; Perrier, Anselme L; Wheelock, Vicki; Cozzi, Emanuele; Martin, Unai Perpiña; Salado-Manzano, Cristina; Mills, Laura J; Drew, Cheney; Goldman, Steven A; Canals, Josep M; Thompson, Leslie M

Cell Therapy for Huntington's Disease: Learning from Failure

亨廷顿病细胞疗法:从失败中吸取教训

Rosser, Anne E; Busse, Monica; Aron Badin, Romina; Canals, Josep M; Wheelock, Vicki; Perrier, Anselme L; Gray, William; Thompson, Leslie; Goldman, Steven

Genotyping single nucleotide polymorphisms for allele-selective therapy in Huntington disease

亨廷顿病等位基因选择性治疗的单核苷酸多态性基因分型

Claassen, Daniel O; Corey-Bloom, Jody; Dorsey, E Ray; Edmondson, Mary; Kostyk, Sandra K; LeDoux, Mark S; Reilmann, Ralf; Rosas, H Diana; Walker, Francis; Wheelock, Vicki; Svrzikapa, Nenad; Longo, Kenneth A; Goyal, Jaya; Hung, Serena; Panzara, Michael A

A randomized, double-blind, placebo-controlled trial of coenzyme Q10 in Huntington disease

一项关于辅酶Q10治疗亨廷顿病的随机、双盲、安慰剂对照试验

McGarry, Andrew; McDermott, Michael; Kieburtz, Karl; de Blieck, Elisabeth A; Beal, Flint; Marder, Karen; Ross, Christopher; Shoulson, Ira; Gilbert, Peter; Mallonee, William M; Guttman, Mark; Wojcieszek, Joanne; Kumar, Rajeev; LeDoux, Mark S; Jenkins, Mary; Rosas, H Diana; Nance, Martha; Biglan, Kevin; Como, Peter; Dubinsky, Richard M; Shannon, Kathleen M; O'Suilleabhain, Padraig; Chou, Kelvin; Walker, Francis; Martin, Wayne; Wheelock, Vicki L; McCusker, Elizabeth; Jankovic, Joseph; Singer, Carlos; Sanchez-Ramos, Juan; Scott, Burton; Suchowersky, Oksana; Factor, Stewart A; Higgins, Donald S Jr; Molho, Eric; Revilla, Fredy; Caviness, John N; Friedman, Joseph H; Perlmutter, Joel S; Feigin, Andrew; Anderson, Karen; Rodriguez, Ramon; McFarland, Nikolaus R; Margolis, Russell L; Farbman, Eric S; Raymond, Lynn A; Suski, Valerie; Kostyk, Sandra; Colcher, Amy; Seeberger, Lauren; Epping, Eric; Esmail, Sherali; Diaz, Nancy; Fung, Wai Lun Alan; Diamond, Alan; Frank, Samuel; Hanna, Philip; Hermanowicz, Neal; Dure, Leon S; Cudkowicz, Merit

Allele-Specific Reduction of the Mutant Huntingtin Allele Using Transcription Activator-Like Effectors in Human Huntington's Disease Fibroblasts.

利用转录激活因子样效应物在人类亨廷顿病成纤维细胞中特异性降低突变亨廷顿等位基因

Fink Kyle D, Deng Peter, Gutierrez Josh, Anderson Joseph S, Torrest Audrey, Komarla Anvita, Kalomoiris Stefanos, Cary Whitney, Anderson Johnathon D, Gruenloh William, Duffy Alexandra, Tempkin Teresa, Annett Geralyn, Wheelock Vicki, Segal David J, Nolta Jan A

Developing stem cell therapies for juvenile and adult-onset Huntington's disease

开发用于治疗青少年和成人发病型亨廷顿病的干细胞疗法

Fink, Kyle D; Deng, Peter; Torrest, Audrey; Stewart, Heather; Pollock, Kari; Gruenloh, William; Annett, Geralyn; Tempkin, Teresa; Wheelock, Vicki; Nolta, Jan A

Predictors of HVOT performance in Parkinson's disease

帕金森病患者HVOT表现的预测因素

Higginson, Christopher I; Wheelock, Vicki L; Levine, Dawn; Pappas, Conrad T E; Sigvardt, Karen A