β-globin gene transfer to human bone marrow for sickle cell disease
β-珠蛋白基因转移至人类骨髓治疗镰状细胞病
期刊:Journal of Clinical Investigation
影响因子:13.3
doi:10.1172/JCI67930
Zulema Romero, Fabrizia Urbinati, Sabine Geiger, Aaron R Cooper, Jennifer Wherley, Michael L Kaufman, Roger P Hollis, Rafael Ruiz de Assin, Shantha Senadheera, Arineh Sahagian, Xiangyang Jin, Alyse Gellis, Xiaoyan Wang, David Gjertson, Satiro Deoliveira, Pamela Kempert, Sally Shupien, Hisham Abdel-A