Small molecule splicing modifiers with systemic HTT-lowering activity
具有系统性降低 HTT 活性的小分子剪接修饰剂
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-021-27157-z
Anuradha Bhattacharyya, Christopher R Trotta, Jana Narasimhan, Kari J Wiedinger, Wencheng Li, Kerstin A Effenberger, Matthew G Woll, Minakshi B Jani, Nicole Risher, Shirley Yeh, Yaofeng Cheng, Nadiya Sydorenko, Young-Choon Moon, Gary M Karp, Marla Weetall, Amal Dakka, Vijayalakshmi Gabbeta, Nikolai
