日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Clinically translatable mitochondrial gene therapy in muscle using tandem mtZFN architecture.

利用串联 mtZFN 结构在肌肉中进行临床转化线粒体基因治疗

Nash Pavel A, Turner Keira M, Powell Christopher A, Van Haute Lindsey, Silva-Pinheiro Pedro, Bubeck Felix, Wiedtke Ellen, Marques Eloïse, Ryan Dylan G, Grimm Dirk, Gammage Payam A, Minczuk Michal

Seroprevalence of binding and neutralizing antibodies against 18 adeno-associated virus types in patients with neuromuscular disorders

神经肌肉疾病患者体内针对18种腺相关病毒的结合抗体和中和抗体的血清阳性率

Wang, Xiaoyan; Klann, Patrick Julian; Wiedtke, Ellen; Sano, Yumi; Fischer, Nico; Schiller, Lisa; Elfert, Anna; Güttsches, Anne-Katrin; Weyen, Ute; Grimm, Dirk; Vorgerd, Matthias; Bayer, Wibke

Robust RNAi enhancement via human Argonaute-2 overexpression from plasmids, viral vectors and cell lines.

通过质粒、病毒载体和细胞系过表达人Argonaute-2,实现强大的RNAi增强

Börner Kathleen, Niopek Dominik, Cotugno Gabriella, Kaldenbach Michaela, Pankert Teresa, Willemsen Joschka, Zhang Xian, Schürmann Nina, Mockenhaupt Stefan, Serva Andrius, Hiet Marie-Sophie, Wiedtke Ellen, Castoldi Mirco, Starkuviene Vytaute, Erfle Holger, Gilbert Daniel F, Bartenschlager Ralf, Boutros Michael, Binder Marco, Streetz Konrad, Kräusslich Hans-Georg, Grimm Dirk

Engineering and evolution of synthetic adeno-associated virus (AAV) gene therapy vectors via DNA family shuffling

通过DNA家族重组对合成腺相关病毒(AAV)基因治疗载体进行工程改造和进化

Kienle, Eike; Senís, Elena; Börner, Kathleen; Niopek, Dominik; Wiedtke, Ellen; Grosse, Stefanie; Grimm, Dirk