日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A differentiated β-globin gene replacement strategy uses heterologous introns to restore physiological expression.

差异化的β-珠蛋白基因替换策略利用异源内含子来恢复生理表达

Wallace Kirby A, Gerstenberg Trevor L, Ennis Craig L, Perez-Bermejo Juan A, Partridge James R, Bandoro Christopher, Matern William M, Andreoletti Gaia, Krassovsky Kristina, Kabir Shaheen, Lalisan Cassandra D, Churi Aishwarya R, Chew Glen M, Corbo Lana, Vincelette Jon E, Klasson Timothy D, Silva Brian J, Strukov Yuri G, Quejarro B Joy, Hill Kaisle A, Treusch Sebastian, Grogan Jane L, Dever Daniel P, Porteus Matthew H, Wienert Beeke

Dual α-globin-truncated erythropoietin receptor knockin restores hemoglobin production in α-thalassemia-derived erythroid cells

双重α-珠蛋白截短型促红细胞生成素受体敲入可恢复α-地中海贫血来源红系细胞的血红蛋白生成

Simon N Chu ,Eric Soupene ,Devesh Sharma ,Roshani Sinha ,Travis McCreary ,Britney Hernandez ,Huifeng Shen ,Beeke Wienert ,Chance Bowman ,Han Yin ,Benjamin J Lesch ,Kun Jia ,Kathleen A Romero ,Zachary Kostamo ,Yankai Zhang ,Tammy Tran ,Marco Cordero ,Shota Homma ,Jessica P Hampton ,James M Gardner ,Bruce R Conklin ,Tippi C MacKenzie ,Vivien A Sheehan ,Matthew H Porteus ,M Kyle Cromer

Dual α-globin and truncated EPO receptor knockin restores hemoglobin production in α-thalassemia-derived red blood cells

双 α 珠蛋白和截短 EPO 受体敲入可恢复 α 地中海贫血衍生红细胞中的血红蛋白生成

Simon N Chu, Eric Soupene, Beeke Wienert, Han Yin, Devesh Sharma, Travis McCreary, Kun Jia, Shota Homma, Jessica P Hampton, James M Gardner, Bruce R Conklin, Tippi C MacKenzie, Matthew H Porteus, M Kyle Cromer

Slow integrin-dependent migration organizes networks of tissue-resident mast cells

缓慢的整合素依赖性迁移组织组织驻留肥大细胞网络

Lukas Kaltenbach #, Paloma Martzloff #, Sarah K Bambach #, Nadim Aizarani, Michael Mihlan, Alina Gavrilov, Katharina M Glaser, Manuel Stecher, Roland Thünauer, Aude Thiriot, Klaus Heger, Katrin Kierdorf, Stephan Wienert, Ulrich H von Andrian, Marc Schmidt-Supprian, Claus Nerlov, Frederick Klauschen,

Identification of novel HPFH-like mutations by CRISPR base editing that elevate the expression of fetal hemoglobin

利用 CRISPR 碱基编辑技术鉴定可提高胎儿血红蛋白表达的新型 HPFH 样突变

Nithin Sam Ravi ,Beeke Wienert ,Stacia K Wyman ,Henry William Bell ,Anila George ,Gokulnath Mahalingam ,Jonathan T Vu ,Kirti Prasad ,Bhanu Prasad Bandlamudi ,Nivedhitha Devaraju ,Vignesh Rajendiran ,Nazar Syedbasha ,Aswin Anand Pai ,Yukio Nakamura ,Ryo Kurita ,Muthuraman Narayanasamy ,Poonkuzhali Balasubramanian ,Saravanabhavan Thangavel ,Srujan Marepally ,Shaji R Velayudhan ,Alok Srivastava ,Mark A DeWitt ,Merlin Crossley ,Jacob E Corn ,Kumarasamypet M Mohankumar

CRISPR nuclease off-target activity and mitigation strategies

CRISPR核酸酶脱靶活性及其缓解策略

Wienert, Beeke; Cromer, M Kyle

Mediating Effects of Mental Health Problems in a Clinical Sample of Adolescents with Obesity

心理健康问题在肥胖青少年临床样本中的中介作用

Hampel, Petra; Stachow, Rainer; Wienert, Julian

Implementing Health Apps for Digital Public Health - An Implementation Science Approach Adopting the Consolidated Framework for Implementation Research

实施健康应用程序以促进数字公共卫生——采用实施科学方法并借鉴实施研究综合框架

Wienert, Julian; Zeeb, Hajo

Enhancing pediatricians' engagement on social media: the role of board style questions

提升儿科医生在社交媒体上的参与度:模拟考试题的作用

Little-Wienert, Kim; Chang, Todd; Agarwal, Rita; Cramton, Rachel; Hillenbrand, Karin; Panchal, Apurva; Stubblefield, Wesley; Mahan, John; Wright, Martha; Donato, Lisa; Chandran, Latha

Timed inhibition of CDC7 increases CRISPR-Cas9 mediated templated repair

定时抑制CDC7可增强CRISPR-Cas9介导的模板修复

Beeke Wienert # ,David N Nguyen # ,Alexis Guenther ,Sharon J Feng ,Melissa N Locke ,Stacia K Wyman ,Jiyung Shin ,Katelynn R Kazane ,Georgia L Gregory ,Matthew A M Carter ,Francis Wright ,Bruce R Conklin ,Alex Marson ,Chris D Richardson ,Jacob E Corn