Interindividual variability in transgene mRNA and protein production following adeno-associated virus gene therapy for hemophilia A
腺相关病毒基因治疗血友病 A 后转基因 mRNA 和蛋白质产生的个体间差异
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/s41591-022-01751-0
Sylvia Fong, Bridget Yates, Choong-Ryoul Sihn, Aras N Mattis, Nina Mitchell, Su Liu, Chris B Russell, Benjamin Kim, Adebayo Lawal, Savita Rangarajan, Will Lester, Stuart Bunting, Glenn F Pierce, K John Pasi, Wing Yen Wong
