日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Syndromic Inborn Errors of Immunity in TREC-Newborn Screening: 5-year Experience from the German Screening Program

TREC新生儿筛查中的综合征性先天性免疫缺陷:德国筛查项目的5年经验

Graafen, Lea; Speckmann, Carsten; Bakhtiar, Shahrzad; Bernuth, Horst V; Lehmberg, Kai; Bader, Peter; Baumann, Ulrich; Beier, Rita; Borte, Stephan; Brockow, Inken; Davies, E Graham; Hartmann, Maximilian; Holzer, Ursula; Klemann, Christian; Kreins, Alexandra Y; Krüger, Renate; Kontny, Udo; Laws, Hans-Jürgen; Meinhardt, Andrea; Morbach, Henner; Naumann-Bartsch, Nora; Rothoeft, Tobias; Schneider, Dominik T; Willasch, Andre; Worth, Austen; Seidel, Markus G; Albert, Michael H; Ehl, Stephan; Hauck, Fabian; Hönig, Manfred; Schulz, Ansgar; Schuetz, Catharina; Ghosh, Sujal

Case report: Advanced age at transplantation and pre-emptive treatment with dupilumab in DOCK8 deficiency

病例报告:DOCK8 缺陷患者移植时年龄较大,并接受度普利尤单抗预防性治疗

Trombello, Sophia; Jarisch, Andrea; Willasch, Andre; Rettinger, Eva; Fekadu-Siebald, Julia; Holzinger, Dirk; Adelmann, Roland; Bader, Peter; Bakhtiar, Shahrzad

Impaired IL-23-dependent induction of IFN-γ underlies mycobacterial disease in patients with inherited TYK2 deficiency

遗传性TYK2缺陷患者的结核分枝杆菌感染是由IL-23依赖性IFN-γ诱导受损引起的。

Masato Ogishi #,Andrés Augusto Arias # ,Rui Yang #,Ji Eun Han #,Peng Zhang,Darawan Rinchai,Joshua Halpern,Jeanette Mulwa,Narelle Keating,Maya Chrabieh,Candice Lainé,Yoann Seeleuthner,Noé Ramírez-Alejo,Nioosha Nekooie-Marnany,Andrea Guennoun,Ingrid Muller-Fleckenstein,Bernhard Fleckenstein,Sara S Kilic,Yoshiyuki Minegishi,Stephan Ehl,Petra Kaiser-Labusch,Yasemin Kendir-Demirkol,Flore Rozenberg,Abderrahmane Errami,Shen-Ying Zhang ,Qian Zhang ,Jonathan Bohlen,Quentin Philippot,Anne Puel ,Emmanuelle Jouanguy ,Zahra Pourmoghaddas #,Shahrzad Bakhtiar #,Andre M Willasch #,Gerd Horneff #,Genevieve Llanora #,Lynette P Shek #,Louis Y A Chai # ,Sen Hee Tay #,Hamid H Rahimi #,Seyed Alireza Mahdaviani #,Serdar Nepesov #,Aziz A Bousfiha #,Emine Hafize Erdeniz #,Adem Karbuz #,Nico Marr #,Carmen Navarrete #,Mehdi Adeli #,Lennart Hammarstrom # ,Hassan Abolhassani #,Nima Parvaneh #,Saleh Al Muhsen #,Mohammed F Alosaimi #,Fahad Alsohime #,Maryam Nourizadeh #,Mostafa Moin #,Rand Arnaout #,Saad Alshareef #,Jamila El-Baghdadi #,Ferah Genel #,Roya Sherkat #,Ayça Kiykim #,Esra Yücel #,Sevgi Keles #,Jacinta Bustamante # ,Laurent Abel # ,Jean-Laurent Casanova # ,Stéphanie Boisson-Dupuis #

Impaired IL-23-dependent induction of IFN-γ underlies mycobacterial disease in patients with inherited TYK2 deficiency

遗传性TYK2缺陷患者的结核分枝杆菌感染是由IL-23依赖性IFN-γ诱导受损引起的。

Masato Ogishi # ,Andrés Augusto Arias # ,Rui Yang # ,Ji Eun Han # ,Peng Zhang ,Darawan Rinchai ,Joshua Halpern ,Jeanette Mulwa ,Narelle Keating ,Maya Chrabieh ,Candice Lainé ,Yoann Seeleuthner ,Noé Ramírez-Alejo ,Nioosha Nekooie-Marnany ,Andrea Guennoun ,Ingrid Muller-Fleckenstein ,Bernhard Fleckenstein ,Sara S Kilic ,Yoshiyuki Minegishi ,Stephan Ehl ,Petra Kaiser-Labusch ,Yasemin Kendir-Demirkol ,Flore Rozenberg ,Abderrahmane Errami ,Shen-Ying Zhang ,Qian Zhang ,Jonathan Bohlen ,Quentin Philippot ,Anne Puel ,Emmanuelle Jouanguy ,Zahra Pourmoghaddas # ,Shahrzad Bakhtiar # ,Andre M Willasch # ,Gerd Horneff # ,Genevieve Llanora # ,Lynette P Shek # ,Louis Y A Chai # ,Sen Hee Tay # ,Hamid H Rahimi # ,Seyed Alireza Mahdaviani # ,Serdar Nepesov # ,Aziz A Bousfiha # ,Emine Hafize Erdeniz # ,Adem Karbuz # ,Nico Marr # ,Carmen Navarrete # ,Mehdi Adeli # ,Lennart Hammarstrom # ,Hassan Abolhassani # ,Nima Parvaneh # ,Saleh Al Muhsen # ,Mohammed F Alosaimi # ,Fahad Alsohime # ,Maryam Nourizadeh # ,Mostafa Moin # ,Rand Arnaout # ,Saad Alshareef # ,Jamila El-Baghdadi # ,Ferah Genel # ,Roya Sherkat # ,Ayça Kiykim # ,Esra Yücel # ,Sevgi Keles # ,Jacinta Bustamante # ,Laurent Abel # ,Jean-Laurent Casanova # ,Stéphanie Boisson-Dupuis #

Correction: Myeloablative conditioning for allo-HSCT in pediatric ALL: FTBI or chemotherapy?-A multicenter EBMT-PDWP study

更正:儿童急性淋巴细胞白血病异基因造血干细胞移植的清髓预处理:全脑照射还是化疗?——一项多中心EBMT-PDWP研究

Willasch, Andre Manfred; Peters, Christina; Sedláček, Petr; Dalle, Jean-Hugues; Kitra-Roussou, Vassiliki; Yesilipek, Akif; Wachowiak, Jacek; Lankester, Arjan; Prete, Arcangelo; Hamidieh, Amir Ali; Ifversen, Marianne; Buechner, Jochen; Kriván, Gergely; Hamladji, Rose-Marie; Diaz-de-Heredia, Cristina; Skorobogatova, Elena; Michel, Gérard; Locatelli, Franco; Bertaina, Alice; Veys, Paul; Dupont, Sophie; Or, Reuven; Güngör, Tayfun; Aleinikova, Olga; Sufliarska, Sabina; Sundin, Mikael; Rascon, Jelena; Kaare, Ain; Nemet, Damir; Fagioli, Franca; Klingebiel, Thomas Erich; Styczynski, Jan; Bierings, Marc; Nagy, Kálmán; Abecasis, Manuel; Afanasyev, Boris; Ansari, Marc; Vettenranta, Kim; Alseraihy, Amal; Chybicka, Alicja; Robinson, Stephen; Bertrand, Yves; Kupesiz, Alphan; Ghavamzadeh, Ardeshir; Campos, Antonio; Pichler, Herbert; Dalissier, Arnaud; Labopin, Myriam; Corbacioglu, Selim; Balduzzi, Adriana; Galimard, Jacques-Emmanuel; Bader, Peter

Myeloablative conditioning for allo-HSCT in pediatric ALL: FTBI or chemotherapy?-A multicenter EBMT-PDWP study

儿童急性淋巴细胞白血病异基因造血干细胞移植的清髓预处理:全脑照射还是化疗?——一项多中心EBMT-PDWP研究

Willasch, Andre Manfred; Peters, Christina; Sedláček, Petr; Dalle, Jean-Hugues; Kitra-Roussou, Vassiliki; Yesilipek, Akif; Wachowiak, Jacek; Lankester, Arjan; Prete, Arcangelo; Hamidieh, Amir Ali; Ifversen, Marianne; Buechner, Jochen; Kriván, Gergely; Hamladji, Rose-Marie; Diaz-de-Heredia, Cristina; Skorobogatova, Elena; Michel, Gérard; Locatelli, Franco; Bertaina, Alice; Veys, Paul; Dupont, Sophie; Or, Reuven; Güngör, Tayfun; Aleinikova, Olga; Sufliarska, Sabina; Sundin, Mikael; Rascon, Jelena; Kaare, Ain; Nemet, Damir; Fagioli, Franca; Klingebiel, Thomas Erich; Styczynski, Jan; Bierings, Marc; Nagy, Kálmán; Abecasis, Manuel; Afanasyev, Boris; Ansari, Marc; Vettenranta, Kim; Alseraihy, Amal; Chybicka, Alicja; Robinson, Stephen; Bertrand, Yves; Kupesiz, Alphan; Ghavamzadeh, Ardeshir; Campos, Antonio; Pichler, Herbert; Dalissier, Arnaud; Labopin, Myriam; Corbacioglu, Selim; Balduzzi, Adriana; Galimard, Jacques-Emmanuel; Bader, Peter

Allogeneic hematopoietic stem cell transplantation from unrelated donors is associated with higher infection rates in children with acute lymphoblastic leukemia-A prospective international multicenter trial on behalf of the BFM-SG and the EBMT-PDWP

来自无关供者的异基因造血干细胞移植与急性淋巴细胞白血病患儿较高的感染率相关——一项由英国骨髓捐献者联合会(BFM-SG)和欧洲骨髓移植协会(EBMT-PDWP)发起的前瞻性国际多中心试验。

Pichler, Herbert; Lawitschka, Anita; Glogova, Evgenia; Willasch, Andre M; von Luettichau, Irene; Lehrnbecher, Thomas; Matthes-Martin, Susanne; Lang, Peter; Bader, Peter; Sykora, Karl W; Schrum, Johanna; Kremens, Bernhard; Ehlert, Karoline; Albert, Michael H; Kuhlen, Michaela; Meisel, Roland; Guengoer, Tayfun; Strahm, Brigitte; Gruhn, Bernd; Schulz, Ansgar; Woessmann, Wilhelm; Poetschger, Ulrike; Peters, Christina

Transplant center practices for psychosocial assessment and management of pediatric hematopoietic stem cell donors

移植中心对儿童造血干细胞捐献者的心理社会评估和管理实践

Wiener, Lori; Hoag, Jennifer A; Pelletier, Wendy; Shah, Nirali N; Shaw, Bronwen E; Pulsipher, Michael A; Bruce, Jessica; Bader, Peter; Willasch, Andre M; Dalissier, Arnaud; Guilcher, Gregory; Anthias, Chloe; Confer, Dennis L; Sees, Jennifer A; Logan, Brent; Switzer, Galen E

Interleukin-15-activated cytokine-induced killer cells may sustain remission in leukemia patients after allogeneic stem cell transplantation: feasibility, safety and first insights on efficacy

白细胞介素-15激活的细胞因子诱导的杀伤细胞可能在异基因造血干细胞移植后维持白血病患者的缓解:可行性、安全性和初步疗效研究

Rettinger, Eva; Huenecke, Sabine; Bonig, Halvard; Merker, Michael; Jarisch, Andrea; Soerensen, Jan; Willasch, Andre; Bug, Gesine; Schulz, Ansgar; Klingebiel, Thomas; Bader, Peter

SMAC Mimetic BV6 Enables Sensitization of Resistant Tumor Cells but also Affects Cytokine-Induced Killer (CIK) Cells: A Potential Challenge for Combination Therapy

SMAC 模拟物 BV6 能够使耐药肿瘤细胞敏感,但也会影响细胞因子诱导的杀伤 (CIK) 细胞:联合治疗的潜在挑战

Eva Rettinger, Andreas Glatthaar, Behnaz Ahangarian Abhari, Sarah Oelsner, Verena Pfirrmann, Sabine Huenecke, Selim Kuçi, Hermann Kreyenberg, Andre M Willasch, Thomas Klingebiel, Simone Fulda, Peter Bader