日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Irradiation- and busulfan-free stem cell transplantation in Fanconi anemia using an anti-CD117 antibody: a phase 1b trial

使用抗CD117抗体治疗范可尼贫血的无辐射、无白消安干细胞移植:一项1b期试验

Agarwal, Rajni; Bertaina, Alice; Soco, Charmaine; Long-Boyle, Janel R; Saini, Gopin; Kunte, Nivedita; Hiroshima, Lyndsie; Chan, Yan Y; Willner, Hana; Krampf, Mark R; Nofal, Rofida; Barbarito, Giulia; Sen, Sushmita; Van Hentenryck, Maite; Walck, Emily; Scheck, Amelia; Perriman, Rhonda J; Bouge, Alisha; Istomina, Elena; Din, Hena Naz; Klinger, Edna F; Cheng, Jerry C; Wlodarski, Marcin W; Boelens, Jaap J; Shizuru, Judith A; Pang, Wendy W; Weinberg, Kenneth; Parkman, Robertson; Roncarolo, Maria Grazia; Porteus, Matthew; Czechowicz, Agnieszka

GFP-on mouse model for interrogation of in vivo gene editing.

用于研究体内基因编辑的 GFP 标记小鼠模型

Dib Carla, Queenan Jack A, Swartzrock Leah, Willner Hana, Denis Morgane, Ahmed Nouraiz, Moulana Zada Fareha, Borges Beltran, Charlesworth Carsten T, Lum Tony, Yates Bradley P, Kwon Caleb Y, Scorzo Augustino V, Davis Scott C, Davis Jessie R, He Ran, Xie Jun, Gao Guangping, MacKenzie Tippi C, Liu David R, Newby Gregory A, Czechowicz Agnieszka D

Targeted hematopoietic stem cell depletion through SCF-blockade

通过SCF阻断靶向清除造血干细胞

Chan, Yan Yi; Ho, Pui Yan; Dib, Carla; Swartzrock, Leah; Rayburn, Maire; Willner, Hana; Ko, Ethan; Ho, Katie; Down, Julian D; Wilkinson, Adam C; Nakauchi, Hiro; Denis, Morgane; Cool, Taylor; Czechowicz, Agnieszka

In utero hematopoietic stem cell transplantation for Fanconi anemia

子宫内造血干细胞移植治疗范可尼贫血

Swartzrock, Leah; Dib, Carla; Denis, Morgane; Willner, Hana; Ho, Katie; Haslett, Ethan; Han, Jian; Pan, Wenjing; Byrne-Steele, Miranda; Brown, Brittany; Krampf, Mark R; Girsen, Anna; Blumenfeld, Yair J; El-Sayed, Yasser Y; Roncarolo, Maria G; MacKenzie, Tippi C; Czechowicz, Agnieszka D