日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intracerebroventricular B7-H3-targeting CAR T cells for diffuse intrinsic pontine glioma: a phase 1 trial

脑室内注射靶向B7-H3的CAR-T细胞治疗弥漫性内生性桥脑胶质瘤:一项I期试验

Vitanza, Nicholas A; Ronsley, Rebecca; Choe, Michelle; Seidel, Kristy; Huang, Wenjun; Rawlings-Rhea, Stephanie D; Beam, Madison; Steinmetzer, Leonel; Wilson, Ashley L; Brown, Christopher; Beebe, Adam; Lindgren, Catherine; Gustafson, Joshua A; Wein, Amy; Holtzclaw, Susan; Hoeppner, Corrine; Goldstein, Hannah E; Browd, Samuel R; Hauptman, Jason S; Lee, Amy; Ojemann, Jeffrey G; Crotty, Erin E; Leary, Sarah E S; Perez, Francisco A; Wright, Jason N; Alonso, Marta M; Dun, Matthew D; Foster, Jessica B; Hurst, Diana; Kong, Ada; Thomsen, Alison; Orentas, Rimas J; Albert, Catherine M; Pinto, Navin; Annesley, Colleen; Gardner, Rebecca A; Ho, On; Pattabhi, Sowmya; Gust, Juliane; Wendler, Jason P; Park, Julie R; Jensen, Michael C

Multi-modal spatial characterization of tumor immune microenvironments identifies targetable inflammatory niches in diffuse large B cell lymphoma

肿瘤免疫微环境的多模态空间表征可识别弥漫性大B细胞淋巴瘤中可靶向的炎症微环境

Dai, Yibo; Kizhakeyil, Atish; Chihara, Dai; Li, Xubin; Liu, Yunhe; Sainz Zuniga, Tania Patricia; Wilson, Ashley; Henderson, Jared; Vibe, Daniil; Petrosyants, Arman; Jacobson, Connor; Sarachakov, Alexander; Nomie, Krystle; Kryukov, Kirill; Bagaev, Aleksander; Chauhan, Ayushi; Westin, Jason R; Flowers, Christopher R; Vega, Francisco; Wang, Linghua; Green, Michael R

Outcomes of PLAT-02 and PLAT-03: evaluating CD19 CAR T-cell therapy and CD19-expressing T-APC support in pediatric B-ALL

PLAT-02 和 PLAT-03 研究结果:评估 CD19 CAR T 细胞疗法和表达 CD19 的 T-APC 支持治疗儿童 B 细胞急性淋巴细胞白血病 (B-ALL) 的疗效

Annesley, Colleen; Seidel, Kristy; Wu, Qian; Summers, Corinne; Wayne, Alan S; Pulsipher, Michael A; Agrawal, Anurag K; Brown, Chris T; Mgebroff, Stephanie; Lindgren, Catherine; Rawlings-Rhea, Stephanie; Huang, Wenjun; Wilson, Ashley L; Jensen, Michael C; Park, Julie R; Gardner, Rebecca A

Blunted CD40-responsive enhancer activation in CREBBP-mutant lymphomas can be restored by enforced CD4 T-cell engagement

CREBBP突变淋巴瘤中CD40反应性增强子激活减弱可通过强制CD4 T细胞参与来恢复。

Yang, Haopeng; Zhang, Wenchao; Ravanmehr, Vida; Cui, Guiling; Bowman, Kevin; Chen, Ruidong; Henderson, Jared M; Lockman, Shyanne; Rojas, Estela; Wilson, Ashley; Parsons, Sydney; Mechaly, Ariel; Regad, Leslie; Haouz, Ahmed; Flowers, Christopher R; Neelapu, Sattva; Nastoupil, Loretta; Davis, R Eric; Deng, Qing; Rodrigues-Lima, Fernando; Green, Michael R

Locoregional infusion of EGFR806-CAR T cells for recurrent or refractory pediatric CNS tumors: Results of the completed BrainChild02 phase 1 clinical trial

局部区域输注EGFR806-CAR T细胞治疗复发性或难治性儿童中枢神经系统肿瘤:已完成的BrainChild02 I期临床试验结果

Gust, Juliane; Cole, Bonnie L; Ronsley, Rebecca; Wilson, Ashley L; Seidel, Kristy; Wendler, Jason; Pattabhi, Sowmya; Brown, Christopher; Rawlings-Rhea, Stephanie D; Shtanukhina, Nadezhda; Browd, Samuel R; Hauptman, Jason S; Lee, Amy; Ojemann, Jeffrey G; Crotty, Erin E; Leary, Sarah E S; Perez, Francisco A; Wright, Jason N; Albert, Catherine M; Pinto, Navin; Gardner, Rebecca A; Vitanza, Nicholas A; Jensen, Michael C; Park, Julie R

Rare variants in BMAL1 are associated with a neurodevelopmental syndrome

BMAL1基因的罕见变异与一种神经发育综合征相关。

Cuddapah, Vishnu Anand; Chen, Dechun; Cho, Bumsik; Moore, Rebecca; Suri, Mohnish; Safraou, Hana; Tran-Mau-Them, Frederic; Wilson, Ashley; Odgis, Jacqueline; Rehman, Atteeq U; Saunders, Carol; Ganesan, Shiva; Jobanputra, Vaidehi; Scherer, Stephen W; Helbig, Ingo; Sehgal, Amita

Feasibility and favorable responses after investigational CAR T-cell therapy for relapsed and refractory infant ALL

研究性 CAR-T 细胞疗法治疗复发难治性婴儿急性淋巴细胞白血病的可行性及良好疗效

Annesley, Colleen; Lamble, Adam; Summers, Corinne; Pulsipher, Michael A; Wayne, Alan S; Rivers, Julie; Huang, Wenjun; Wilson, Ashley; Wu, Qian Vicky; Seidel, Kristy; Mgebroff, Stephanie; Brown, Christopher; Lindgren, Catherine; Park, Julie R; Jensen, Michael; Gardner, Rebecca

Spliceosome malfunction causes neurodevelopmental disorders with overlapping features

剪接体功能障碍会导致具有重叠特征的神经发育障碍。

Li, Dong; Wang, Qin; Bayat, Allan; Battig, Mark R; Zhou, Yijing; Bosch, Daniëlle Gm; van Haaften, Gijs; Granger, Leslie; Petersen, Andrea K; Pérez-Jurado, Luis A; Aznar-Laín, Gemma; Aneja, Anushree; Hancarova, Miroslava; Bendova, Sarka; Schwarz, Martin; Kremlikova Pourova, Radka; Sedlacek, Zdenek; Keena, Beth A; March, Michael E; Hou, Cuiping; O'Connor, Nora; Bhoj, Elizabeth J; Harr, Margaret H; Lemire, Gabrielle; Boycott, Kym M; Towne, Meghan; Li, Megan; Tarnopolsky, Mark; Brady, Lauren; Parker, Michael J; Faghfoury, Hanna; Parsley, Lea Kristin; Agolini, Emanuele; Dentici, Maria Lisa; Novelli, Antonio; Wright, Meredith; Palmquist, Rachel; Lai, Khanh; Scala, Marcello; Striano, Pasquale; Iacomino, Michele; Zara, Federico; Cooper, Annina; Maarup, Timothy J; Byler, Melissa; Lebel, Robert Roger; Balci, Tugce B; Louie, Raymond; Lyons, Michael; Douglas, Jessica; Nowak, Catherine; Afenjar, Alexandra; Hoyer, Juliane; Keren, Boris; Maas, Saskia M; Motazacker, Mahdi M; Martinez-Agosto, Julian A; Rabani, Ahna M; McCormick, Elizabeth M; Falk, Marni J; Ruggiero, Sarah M; Helbig, Ingo; Møller, Rikke S; Tessarollo, Lino; Tomassoni Ardori, Francesco; Palko, Mary Ellen; Hsieh, Tzung-Chien; Krawitz, Peter M; Ganapathi, Mythily; Gelb, Bruce D; Jobanputra, Vaidehi; Wilson, Ashley; Greally, John; Jacquemont, Sébastien; Jizi, Khadijé; Bruel, Ange-Line; Quelin, Chloé; Misra, Vinod K; Chick, Erika; Romano, Corrado; Greco, Donatella; Arena, Alessia; Morleo, Manuela; Nigro, Vincenzo; Seyama, Rie; Uchiyama, Yuri; Matsumoto, Naomichi; Taira, Ryoji; Tashiro, Katsuya; Sakai, Yasunari; Yigit, Gökhan; Wollnik, Bernd; Wagner, Michael; Kutsche, Barbara; Hurst, Anna Ce; Thompson, Michelle L; Schmidt, Ryan; Randolph, Linda; Spillmann, Rebecca C; Shashi, Vandana; Higginbotham, Edward J; Cordeiro, Dawn; Carnevale, Amanda; Costain, Gregory; Khan, Tayyaba; Funalot, Benoît; Tran Mau-Them, Frederic; Fernandez Garcia Moya, Luis; García-Miñaúr, Sixto; Osmond, Matthew; Chad, Lauren; Quercia, Nada; Carrasco, Diana; Li, Chumei; Sanchez-Valle, Amarilis; Kelley, Meghan; Nizon, Mathilde; Jensson, Brynjar O; Sulem, Patrick; Stefansson, Kari; Gorokhova, Svetlana; Busa, Tiffany; Rio, Marlène; Hadj Habdallah, Hamza; Lesieur-Sebellin, Marion; Amiel, Jeanne; Pingault, Véronique; Mercier, Sandra; Vincent, Marie; Philippe, Christophe; Fatus-Fauconnier, Clemence; Friend, Kathryn; Halligan, Rebecca K; Biswas, Sunita; Rosser, Jane; Shoubridge, Cheryl; Corbett, Mark; Barnett, Christopher; Gecz, Jozef; Leppig, Kathleen; Slavotinek, Anne; Marcelis, Carlo; Pfundt, Rolph; de Vries, Bert Ba; van Slegtenhorst, Marjon A; Brooks, Alice S; Cogne, Benjamin; Rambaud, Thomas; Tümer, Zeynep; Zackai, Elaine H; Akizu, Naiara; Song, Yuanquan; Hakonarson, Hakon

Cell-Free DNA Analysis for the Determination of Fetal Red Blood Cell Antigen Genotype in Individuals With Alloimmunized Pregnancies

利用无细胞DNA分析法测定同种免疫妊娠患者胎儿红细胞抗原基因型

Rego, Shannon; Ashimi Balogun, Olaide; Emanuel, Kirsten; Overcash, Rachael; Gonzalez, Juan M; Denomme, Gregory A; Hoskovec, Jennifer; King, Haley; Wilson, Ashley; Wynn, Julia; Moise, Kenneth J Jr

Cancer prognosis information-seeking among survivors and caregivers: findings from the National Cancer Institute's Cancer Information Service

癌症幸存者及其照护者寻求癌症预后信息的情况:来自美国国家癌症研究所癌症信息服务中心的调查结果

Wilson, Ashley; Huang, Grace; Kueppers, George; Dwyer, Laura A; Han, Paul K J; Vanderpool, Robin C