日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

The N=1 Collaborative: advancing customized nucleic acid therapies through collaboration and data sharing

N=1协作项目:通过合作和数据共享推进定制化核酸疗法

Belgrad, Jillian; McConnell, Erin; Leonard, Stef; Nolen, Nicole; Lauffer, Marlen C; Watts, Jonathan K; Yu, Timothy; Yan, Winston X; Aartsma-Rus, Annemieke

Structural basis for target DNA cleavage and guide RNA processing by CRISPR-Casλ2

CRISPR-Casλ2 靶DNA切割和引导RNA加工的结构基础

Omura, Satoshi N; Alfonse, Lauren E; Ornstein, Alexa; Morinaga, Hayato; Hirano, Hisato; Itoh, Yuzuru; Munoz, Gabrielle; Garrity, Anthony J; Hoffman, Gregory R; DiTommaso, Tia; Yan, Winston X; Cheng, David R; Scott, David A; Maben, Zachary; Nureki, Osamu

Initial Characterization of 12 New Subtypes and Variants of Type V CRISPR Systems

对12种新型V型CRISPR系统亚型和变体的初步表征

Tordoff, Jesse; Alfonse, Lauren E; Makarova, Kira S; Ornstein, Alexa; Garrity, Anthony J; Yan, Winston X; Scott, David A; Koonin, Eugene V; Cheng, David R

Consensus Guidelines for the Design and In Vitro Preclinical Efficacy Testing N-of-1 Exon Skipping Antisense Oligonucleotides

N-of-1外显子跳跃反义寡核苷酸的设计和体外临床前疗效测试共识指南

Aartsma-Rus, Annemieke; Garanto, Alejandro; van Roon-Mom, Willeke; McConnell, Erin M; Suslovitch, Victoria; Yan, Winston X; Watts, Jonathan K; Yu, Timothy W

Engineered Cas12i2 is a versatile high-efficiency platform for therapeutic genome editing

工程化Cas12i2是一种用途广泛、高效的治疗性基因组编辑平台。

Colin McGaw # ,Anthony J Garrity # ,Gabrielle Z Munoz ,Jeffrey R Haswell ,Sejuti Sengupta ,Elise Keston-Smith ,Pratyusha Hunnewell ,Alexa Ornstein ,Mishti Bose ,Quinton Wessells ,Noah Jakimo ,Paul Yan ,Huaibin Zhang ,Lauren E Alfonse ,Roy Ziblat ,Jason M Carte ,Wei-Cheng Lu ,Derek Cerchione ,Brendan Hilbert ,Shanmugapriya Sothiselvam ,Winston X Yan ,David R Cheng ,David A Scott ,Tia DiTommaso ,Shaorong Chong

CRISPR-Cas in mobile genetic elements: counter-defence and beyond

CRISPR-Cas 在移动遗传元件中的应用:反防御及其他

Faure, Guilhem; Shmakov, Sergey A; Yan, Winston X; Cheng, David R; Scott, David A; Peters, Joseph E; Makarova, Kira S; Koonin, Eugene V

Cas13d Is a Compact RNA-Targeting Type VI CRISPR Effector Positively Modulated by a WYL-Domain-Containing Accessory Protein

Cas13d 是一种紧凑型 RNA 靶向 VI 型 CRISPR 效应蛋白,其活性受含有 WYL 结构域的辅助蛋白正向调控。

Yan, Winston X; Chong, Shaorong; Zhang, Huaibin; Makarova, Kira S; Koonin, Eugene V; Cheng, David R; Scott, David A

Engineered Cpf1 variants with altered PAM specificities

具有改变的PAM特异性的工程化Cpf1变体

Gao, Linyi; Cox, David B T; Yan, Winston X; Manteiga, John C; Schneider, Martin W; Yamano, Takashi; Nishimasu, Hiroshi; Nureki, Osamu; Crosetto, Nicola; Zhang, Feng

BLISS is a versatile and quantitative method for genome-wide profiling of DNA double-strand breaks

BLISS 是一种用于全基因组 DNA 双链断裂分析的多功能定量方法

Winston X Yan, Reza Mirzazadeh, Silvano Garnerone, David Scott, Martin W Schneider, Tomasz Kallas, Joaquin Custodio, Erik Wernersson, Yinqing Li, Linyi Gao, Yana Federova, Bernd Zetsche, Feng Zhang, Magda Bienko, Nicola Crosetto

In vivo gene editing in dystrophic mouse muscle and muscle stem cells

在营养不良小鼠肌肉和肌肉干细胞中进行体内基因编辑

Tabebordbar, Mohammadsharif; Zhu, Kexian; Cheng, Jason K W; Chew, Wei Leong; Widrick, Jeffrey J; Yan, Winston X; Maesner, Claire; Wu, Elizabeth Y; Xiao, Ru; Ran, F Ann; Cong, Le; Zhang, Feng; Vandenberghe, Luk H; Church, George M; Wagers, Amy J