日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Artificial miRNA-mediated reduction of SNCA for the treatment of α-synucleinopathies.

利用人工 miRNA 介导的 SNCA 减少治疗 α-突触核蛋白病。

Elmer Bradford, Wischhof Erik, Chan Tiffany, Mahendran Thanga Aishwarya, Ardinger Jeff, Richards Brenda, Liu Dongyu, Bladon John H, He Ye, Jackson Robert, Fleming Michael, Rapaport Franck, Khader Shameer, Goulet Martin, Mueller Christian, Ramachandran Shyam

TMEM65-dependent Ca2+ extrusion safeguards mitochondrial homeostasis

TMEM65依赖的Ca2+外排维持线粒体稳态

Massimo Vetralla,Lena Wischhof #,Asrat Kahsay #,Vanessa Cadenelli,Enzo Scifo,Beijia Xie,Miriana Sbrissa,Maëlle Sandhira Habert,Dan Ehninger,Rosario Rizzuto,Daniele Bano,Diego De Stefani

Cross-species efficacy of AAV-mediated ARSA replacement for metachromatic leukodystrophy

AAV介导的ARSA替代疗法治疗异染性脑白质营养不良的跨物种疗效

Ramachandran, Shyam; Ardinger, Jeffery; Bu, Jie; Ramos, MiAngela; Guo, Lilu; Ghosh, Dhiman; Hossain, Mahmud; Chou, Shih-Ching; Chen, Yao; Wischhof, Erik; Ayloo, Swathi; Trullo, Roger; Luo, Yuxia; Hogestyn, Jessica M; DuBreuil, Daniel M; Crosier, Emily; Flyer-Adams, Johanna G; Richards, Amy M; Tsabar, Michael; Gaglia, Giorgio; Nass, Shelley; Nambiar, Bindu; Woodcock, Denise; O'Riordan, Catherine; Tang, Qi; Elmer, Bradford; Zhang, Bailin; Goulet, Martin; Mueller, Christian

AAV delivery of artificial miRNA targeting MAPT for the reduction of tau pathology in Alzheimer's disease

利用腺相关病毒载体递送靶向MAPT的人工miRNA以减少阿尔茨海默病中的tau蛋白病理

Hogestyn, Jessica M; Wischhof, Erik; Chen, Yao; Chan, Tiffany; Richards, Brenda; Mahendran, Thangaaishwarya; Adams, Johanna; Dubreuil, Daniel; Bu, Jie; Jackson, Robert; Goulet, Martin; Mueller, Christian; Ramachandran, Shyam; Elmer, Bradford

Microglia rescue neurons from aggregate-induced neuronal dysfunction and death through tunneling nanotubes

小胶质细胞通过隧道纳米管拯救因聚集引起的神经元功能障碍和死亡

Hannah Scheiblich, Frederik Eikens, Lena Wischhof, Sabine Opitz, Kay Jüngling, Csaba Cserép, Susanne V Schmidt, Jessica Lambertz, Tracy Bellande, Balázs Pósfai, Charlotte Geck, Jasper Spitzer, Alexandru Odainic, Sergio Castro-Gomez, Stephanie Schwartz, Ibrahim Boussaad, Rejko Krüger, Enrico Glaab, D

METB-09. VARIANT WORKBENCH IN THE KIDS FIRST PROGRAM FACILITATES GENOMIC DISCOVERIES IN PEDIATRIC NEURO-ONCOLOGY RESEARCH

METB-09. 儿童优先计划中的变异工作台促进了儿科神经肿瘤学研究中的基因组学发现

Wischhof, Lena; Lee, Hang-Mao; Tutas, Janine; Overkott, Clemens; Tedt, Eileen; Stork, Miriam; Peitz, Michael; Brüstle, Oliver; Ulas, Thomas; Händler, Kristian; Schultze, Joachim L; Ehninger, Dan; Nicotera, Pierluigi; Salomoni, Paolo; Bano, Daniele; Guo, Yiran; Li, Qi; Rozowsky, Jare; Costanza, Jeremy; Mattioni, Michele; Thibert, Jean-Philippe; Brown, Miguel; Higgins, David; Zhu, Yuankun; Heath, Allison; Resnick, Adam; Ferretti, Vincent

Actin-nucleation promoting factor N-WASP influences alpha-synuclein condensates and pathology

肌动蛋白成核促进因子 N-WASP 影响 α-突触核蛋白凝聚物和病理

Joshua Jackson #, Christian Hoffmann #, Enzo Scifo #, Han Wang, Lena Wischhof, Antonia Piazzesi, Mrityunjoy Mondal, Hanna Shields, Xuesi Zhou, Magali Mondin, Eanna B Ryan, Hermann Döring, Jochen H M Prehn, Klemens Rottner, Gregory Giannone, Pierluigi Nicotera, Dan Ehninger, Dragomir Milovanovic, Dan

Mitochondrial complex I inhibition enhances astrocyte responsiveness to pro-inflammatory stimuli

线粒体复合物 I 抑制可增强星形胶质细胞对促炎刺激的反应

Lena Wischhof, Amal John Mathew, Lorenzo Bonaguro, Marc Beyer, Dan Ehninger, Pierluigi Nicotera, Daniele Bano

AIFM1 beyond cell death: An overview of this OXPHOS-inducing factor in mitochondrial diseases

AIFM1在细胞死亡之外的作用:线粒体疾病中这种氧化磷酸化诱导因子的概述

Wischhof, Lena; Scifo, Enzo; Ehninger, Dan; Bano, Daniele

BCL7A-containing SWI/SNF/BAF complexes modulate mitochondrial bioenergetics during neural progenitor differentiation

含有 BCL7A 的 SWI/SNF/BAF 复合物在神经祖细胞分化过程中调节线粒体生物能量学

Lena Wischhof, Hang-Mao Lee, Janine Tutas, Clemens Overkott, Eileen Tedt, Miriam Stork, Michael Peitz, Oliver Brüstle, Thomas Ulas, Kristian Händler, Joachim L Schultze, Dan Ehninger, Pierluigi Nicotera, Paolo Salomoni, Daniele Bano