Indirect treatment comparison of iptacopan versus pegcetacoplan for patients with paroxysmal nocturnal hemoglobinuria and residual anemia despite C5 inhibitor treatment
对接受C5抑制剂治疗后仍存在残余贫血的阵发性睡眠性血红蛋白尿患者,比较iptacopan与pegcetacoplan的间接治疗效果
期刊:Journal of Comparative Effectiveness Research
影响因子:2.5
doi:10.57264/cer-2025-0167
Kulasekararaj, Austin; Scheinberg, Phillip; Balp, Maria-Magdalena; Somenzi, Olivier; Wiyani, Anggie; Snellman, Josefin; Walsh, Sarah; Pannagl, Katharina; Steenkamp, Jason; de Latour, Régis Peffault