日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Beyond motor neurons: autonomic dysfunction and ECG findings in adults with 5q-spinal muscular atrophy

超越运动神经元:5q-脊髓性肌萎缩症成人患者的自主神经功能障碍和心电图表现

Bacara, Kaan; Stojanovic, Stevan D; Wohnrade, Camilla; Osmanovic, Alma; Schreiber-Katz, Olivia; Haghikia, Aiden; Petri, Susanne; Bjelica, Bogdan

Compound Muscle Action Potential (CMAP) Amplitude Trajectories and Pattern in Adults with 5q-Spinal Muscular Atrophy Receiving Nusinersen Therapy: A Multicenter, Binational Observational Study

接受诺西那生治疗的5q-脊髓性肌萎缩症成人患者的复合肌肉动作电位(CMAP)振幅轨迹和模式:一项多中心、跨国观察性研究

Bjelica, Bogdan; Wohnrade, Camilla; Osmanovic, Alma; Schreiber-Katz, Olivia; Koerner, Sonja; Kollewe, Katja; Haeckl, Sebastian; Freigang, Maren; Cordts, Isabell; Becker, Benedikt; Vogt, Charlotte; Muhandes, Mohamad Tareq; Günther, René; Deschauer, Marcus; Koch, Jan C; Tuerk, Matthias; Regensburger, Martin; Neuwirth, Christoph; Petri, Susanne

Respiratory function in 192 adult patients with spinal muscular atrophy (SMA) treated with nusinersen - a multicenter observational study

一项多中心观察性研究:192例接受诺西那生治疗的脊髓性肌萎缩症(SMA)成年患者的呼吸功能

Wurster, Claudia D; Stolte, Benjamin; Kessler, Tobias; Freigang, Maren; Bjelica, Bogdan; Ilse, Benjamin; Koch, Jan C; Cordts, Isabell; Mensch, Alexander; Zeller, Daniel; Uzelac, Zeljko; Sam, Georges; Lapp, Hanna Sophie; Wohnrade, Camilla; Rödiger, Annekathrin; Muhandes, Mohamad Tareq; Schneider, Ilka; Bellut, Julia; Nentwich, Julia; Dorst, Johannes; Schuster, Joachim; Schreiber-Katz, Olivia; Osmanovic, Alma; Totzeck, Andreas; Thimm, Andreas; Steinbach, Robert; Grosskreutz, Julian; Kleinschnitz, Christoph; Ludolph, Albert C; Deschauer, Marcus; Kirschner, Janbernd; Dreyhaupt, Jens; Wollinsky, Kurt; Petri, Susanne; Weiler, Markus; Hagenacker, Tim; Günther, René

Unraveling the Heterogeneity of ALS-A Call to Redefine Patient Stratification for Better Outcomes in Clinical Trials

揭示肌萎缩侧索硬化症的异质性——呼吁重新定义患者分层,以在临床试验中获得更好的结果

Tzeplaeff, Laura; Jürs, Alexandra V; Wohnrade, Camilla; Demleitner, Antonia F

Diagnostic value of neurofilaments in differentiating motor neuron disease from multifocal motor neuropathy

神经丝在鉴别运动神经元疾病和多灶性运动神经病中的诊断价值

Wohnrade, Camilla; Seeliger, Tabea; Gingele, Stefan; Bjelica, Bogdan; Skripuletz, Thomas; Petri, Susanne

Risdiplam therapy in adults with 5q-SMA: observational study on motor function and treatment satisfaction

利司他普拉治疗5q-SMA成人患者:运动功能和治疗满意度的观察性研究

Bjelica, Bogdan; Wohnrade, Camilla; Cespedes, Iraima; Osmanovic, Alma; Schreiber-Katz, Olivia; Petri, Susanne

An observational cohort study on pulmonary function in adult patients with 5q-spinal muscular atrophy under nusinersen therapy

一项关于接受诺西那生治疗的5q-脊髓性肌萎缩症成年患者肺功能的观察性队列研究

Bjelica, Bogdan; Wohnrade, Camilla; Osmanovic, Alma; Schreiber-Katz, Olivia; Petri, Susanne