Primary CD34(+) cells of patients with vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic (VEXAS) syndrome are highly sensitive to targeted treatment with TAK-243
患有空泡、E1酶、X连锁、自身炎症性体细胞(VEXAS)综合征的患者的原代CD34(+)细胞对TAK-243靶向治疗高度敏感。
期刊:British Journal of Haematology
影响因子:3.8
doi:10.1111/bjh.70203
Nowak, Daniel; Demmerle, Marie; Klär, Alessa; Streuer, Alexander; Riabov, Vladimir; Altrock, Eva; Rapp, Felicitas; Belzer, Ann-Christin; Klink, Teresa; Hahn, Meret; Hofmann, Franziska; Nowak, Verena; Weimer, Nadine; Obländer, Julia; Palme, Iris; Göl, Melda; Darwich, Ali; Steiner, Laurenz; Abba, Mohammed; Metzgeroth, Georgia; Hofmann, Wolf-Karsten; Schmitt, Nanni