Combining multiomics and drug perturbation profiles to identify muscle-specific treatments for spinal muscular atrophy
结合多组学和药物扰动谱来确定脊髓性肌萎缩症的肌肉特异性治疗方法
期刊:JCI Insight
影响因子:6.3
doi:10.1172/jci.insight.149446
Katharina E Meijboom, Viola Volpato, Jimena Monzón-Sandoval, Joseph M Hoolachan, Suzan M Hammond, Frank Abendroth, Olivier G de Jong, Gareth Hazell, Nina Ahlskog, Matthew Ja Wood, Caleb Webber, Melissa Bowerman