Real-world effectiveness of elexacaftor/tezacaftor/ivacaftor on the burden of illness in adolescents and adults with cystic fibrosis
elexacaftor/tezacaftor/ivacaftor 对囊性纤维化青少年和成人患者疾病负担的真实世界疗效
期刊:Heliyon
影响因子:3.6
doi:10.1016/j.heliyon.2024.e28508
Keens, Thomas; Hoffman, Veena; Topuria, Ia; Elder, Ken; Cerf, Shannon; Mulder, Kyra; Roberts, Jon; Lysinger, Jerimiah; Del Carmen Reyes, Maria; Berdella, Maria; Cairns, Anne Marie; Jain, Manu; Ganapathy, Vaidyanathan; Lou, Yiyue; Morcos, Bassem; Wu, Chuntao; Sass, Laura