日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A novel humanized mouse lacking murine P450 oxidoreductase for studying human drug metabolism

一种缺乏小鼠 P450 氧化还原酶的新型人源化小鼠,用于研究人类药物代谢

Mercedes Barzi, Francis P Pankowicz, Barry Zorman, Xing Liu, Xavier Legras, Diane Yang, Malgorzata Borowiak, Beatrice Bissig-Choisat, Pavel Sumazin, Feng Li, Karl-Dimiter Bissig

Reprogramming metabolic pathways in vivo with CRISPR/Cas9 genome editing to treat hereditary tyrosinaemia

利用 CRISPR/Cas9 基因组编辑技术在体内重编程代谢途径以治疗遗传性酪氨酸血症

Francis P Pankowicz, Mercedes Barzi, Xavier Legras, Leroy Hubert, Tian Mi, Julie A Tomolonis, Milan Ravishankar, Qin Sun, Diane Yang, Malgorzata Borowiak, Pavel Sumazin, Sarah H Elsea, Beatrice Bissig-Choisat, Karl-Dimiter Bissig

Development and rescue of human familial hypercholesterolaemia in a xenograft mouse model

在异种移植小鼠模型中建立和挽救人类家族性高胆固醇血症

Beatrice Bissig-Choisat ,Lili Wang ,Xavier Legras ,Pradip K Saha ,Leon Chen ,Peter Bell ,Francis P Pankowicz ,Matthew C Hill ,Mercedes Barzi ,Claudia Kettlun Leyton ,Hon-Chiu Eastwood Leung ,Robert L Kruse ,Ryan W Himes ,John A Goss ,James M Wilson ,Lawrence Chan ,William R Lagor ,Karl-Dimiter Bissig