CRISPR/Cas9-mediated β-globin gene knockout in rabbits recapitulates human β-thalassemia
利用 CRISPR/Cas9 介导的 β-珠蛋白基因敲除技术在兔中重现了人类 β-地中海贫血症。
期刊:Journal of Biological Chemistry
影响因子:3.9
doi:10.1016/j.jbc.2021.100464
Yang, Yi; Kang, Xiangjin; Hu, Shiqi; Chen, Bangzhu; Xie, Yingjun; Song, Bing; Zhang, Quanjun; Wu, Han; Ou, Zhanhui; Xian, Yexing; Fan, Yong; Li, Xiaoping; Lai, Liangxue; Sun, Xiaofang