Dual-AAV split prime editor corrects the mutation and phenotype in mice with inherited retinal degeneration.
双 AAV 分裂启动编辑器可纠正患有遗传性视网膜变性的小鼠的突变和表型
期刊:Signal Transduction and Targeted Therapy
影响因子:52.7
doi:10.1038/s41392-022-01234-1
She Kaiqin, Liu Yi, Zhao Qinyu, Jin Xiu, Yang Yiliu, Su Jing, Li Ruiting, Song Li, Xiao Jianlu, Yao Shaohua, Lu Fang, Wei Yuquan, Yang Yang