Extracellular nanovesicles for packaging of CRISPR-Cas9 protein and sgRNA to induce therapeutic exon skipping
用于包装 CRISPR-Cas9 蛋白和 sgRNA 以诱导治疗性外显子跳跃的细胞外纳米囊泡
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-020-14957-y
Peter Gee,Mandy S Y Lung,Yuya Okuzaki,Noriko Sasakawa,Takahiro Iguchi,Yukimasa Makita,Hiroyuki Hozumi,Yasutomo Miura,Lucy F Yang,Mio Iwasaki,Xiou H Wang,Matthew A Waller,Nanako Shirai,Yasuko O Abe,Yoko Fujita,Kei Watanabe,Akihiro Kagita,Kumiko A Iwabuchi,Masahiko Yasuda,Huaigeng Xu,Takeshi Noda,Jun Komano,Hidetoshi Sakurai,Naoto Inukai,Akitsu Hotta