Vision rescue via unconstrained in vivo prime editing in degenerating neural retinas
通过对退化神经视网膜进行不受限制的体内基因编辑来挽救视力
期刊:Journal of Experimental Medicine
影响因子:10.6
doi:10.1084/jem.20220776
Qin, Huan; Zhang, Wenliang; Zhang, Shiyao; Feng, Yuan; Xu, Weihui; Qi, Jia; Zhang, Qian; Xu, Chunxiu; Liu, Shanshan; Zhang, Jia; Lei, Yushuang; Liu, Wanqin; Feng, Shuyu; Wang, Jingjing; Fu, Xuefei; Xu, Zifen; Li, Ping; Yao, Kai