Genetically blocking HPD via CRISPR-Cas9 protects against lethal liver injury in a pig model of tyrosinemia type I
通过 CRISPR-Cas9 基因阻断 HPD 可防止 I 型酪氨酸血症猪模型发生致命性肝损伤
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2021.04.002
Peng Gu, Qin Yang, Bangzhu Chen, Ya-Nan Bie, Wen Liu, Yuguang Tian, Hongquan Luo, Tao Xu, Chunjin Liang, Xing Ye, Yan Liu, Xiangwu Tang, Weiwang Gu