Therapeutic benefit of idebenone in patients with Leber hereditary optic neuropathy: The LEROS nonrandomized controlled trial
艾地苯醌治疗莱伯遗传性视神经病变患者的疗效:LEROS非随机对照试验
期刊:Cell Reports Medicine
影响因子:10.6
doi:10.1016/j.xcrm.2024.101437
Yu-Wai-Man, Patrick; Carelli, Valerio; Newman, Nancy J; Silva, Magda Joana; Linden, Aki; Van Stavern, Gregory; Szaflik, Jacek P; Banik, Rudrani; Lubiński, Wojciech; Pemp, Berthold; Liao, Yaping Joyce; Subramanian, Prem S; Misiuk-Hojło, Marta; Newman, Steven; Castillo, Lorena; Kocięcki, Jarosław; Levin, Marc H; Muñoz-Negrete, Francisco Jose; Yagan, Ali; Cherninkova, Sylvia; Katz, David; Meunier, Audrey; Votruba, Marcela; Korwin, Magdalena; Dziedziak, Jacek; Jurkutė, Neringa; Harvey, Joshua P; La Morgia, Chiara; Priglinger, Claudia; Llòria, Xavier; Tomasso, Livia; Klopstock, Thomas